1. 球脊髄性筋萎縮症 Disease details / Clinical trials / Drug dev / DR info

臨床試験数 : 19 / 薬物数 : 16 - (DrugBank : 7) / 標的遺伝子数 : 10 - 標的パスウェイ数 : 18

薬物、開発者（Primary Sponsor）、臨床試験情報（症例登録開始年（Enrollment year）、フェーズ、ID、実施国）
AJ201
   AnnJi Pharmaceutical Co., Ltd.
      2023   Phase 1/Phase 2   NCT05517603   United States
BVS857
   Novartis Farma SpA
      2014   Phase 2   EUCTR2013-002608-15-IT   Denmark;Germany;Italy;United States
   Novartis Pharma Services AG
      2014   Phase 2   EUCTR2013-002608-15-DK   Denmark;Germany;Italy;United States
      2014   Phase 2   EUCTR2013-002608-15-DE   Denmark;Germany;Italy;United States
   Novartis Pharmaceuticals
      2014   Phase 2   NCT02024932   Denmark;Germany;Italy;United States
Clenbuterol
   AZIENDA OSPEDALIERA DI PADOVA
      2010   -   EUCTR2010-022558-18-IT   Italy
   Gianni Soraru
      2024   Phase 2   NCT06169046   Italy
Clenbuterolo
   AZIENDA OSPEDALIERA DI PADOVA
      2021   Phase 2   EUCTR2017-005103-27-IT   Italy
Creatine
   Department of Neurology, Nagoya University Graduate School of Medicine
      2014   -   JPRN-UMIN000012503   Japan
Dutasteride
   National Institute of Neurological Disorders and Stroke (NINDS)
      2006   Phase 2   NCT00303446   United States
Electrophysiologic study
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand
Goserelin
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand
Leuprolide
   National Center for Research Resources (NCRR)
      1992   Phase 2   NCT00004771   -
Leuprorelin acetate
   Department of Neurology Chiba University Graduate School of Medicine
      2008   -   JPRN-UMIN000001455   Japan
   Department of Neurology, Nagoya University School of Medicine
      2003   Phase 2   JPRN-UMIN000000474   Japan
   TAKEDA PHARMACEUTICAL COMPANY LTD.
      2018   -   JPRN-jRCT1080223924   -
   Takeda
      2017   -   NCT03555578   Japan
Mexiletine hydrochloride
   Masahisa Katsuno
      2025   Phase 2/Phase 3   NCT06862596   Japan
   Nagoya University Graduate School of Medicine
      2017   Phase 2   JPRN-UMIN000026150   Japan
Monores 20 MCG 30 compresse
   AZIENDA OSPEDALIERA DI PADOVA
      2021   Phase 2   EUCTR2017-005103-27-IT   Italy
Monores*30CPR 20MCG
   AZIENDA OSPEDALIERA DI PADOVA
      2010   -   EUCTR2010-022558-18-IT   Italy
NIDO-361
   Nido Biosciences, Inc.
      2024   Phase 2   NCT06411912   Denmark;Italy;Korea, Republic of;United Kingdom
Testosterone
   National Center for Research Resources (NCRR)
      1992   Phase 2   NCT00004771   -
Tissue biopsy
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand