122. 脳表ヘモジデリン沈着症 Disease details / Clinical trials / Drug dev / DR info /
臨床試験数 : 4 / 薬物数 : 8 - (DrugBank : 2) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Deferiprone
Department of Neurology, Tokyo Medical and Dental University
2024 - JPRN-UMIN000021218 Japan
Sanjo Nobuo
2019 - JPRN-jRCTs031180438 -
DNA BIO-banking
University College, London
2020 - NCT04200664 United Kingdom
Hearing assessment
University College, London
2020 - NCT04200664 United Kingdom
Inosine
Superficial Siderosis Research Alliance Inc.
2023 - NCT04890808 -
IP6
Superficial Siderosis Research Alliance Inc.
2023 - NCT04890808 -
Olfactory (smell) function testing
University College, London
2020 - NCT04200664 United Kingdom
Quality OF life assessment
University College, London
2020 - NCT04200664 United Kingdom
Vestibular/balance assessment
University College, London
2020 - NCT04200664 United Kingdom
Department of Neurology, Tokyo Medical and Dental University
2024 - JPRN-UMIN000021218 Japan
Sanjo Nobuo
2019 - JPRN-jRCTs031180438 -
DNA BIO-banking
University College, London
2020 - NCT04200664 United Kingdom
Hearing assessment
University College, London
2020 - NCT04200664 United Kingdom
Inosine
Superficial Siderosis Research Alliance Inc.
2023 - NCT04890808 -
IP6
Superficial Siderosis Research Alliance Inc.
2023 - NCT04890808 -
Olfactory (smell) function testing
University College, London
2020 - NCT04200664 United Kingdom
Quality OF life assessment
University College, London
2020 - NCT04200664 United Kingdom
Vestibular/balance assessment
University College, London
2020 - NCT04200664 United Kingdom