131. アレキサンダー病 Disease details / Clinical trials / Drug dev / DR info /


臨床試験数 : 4 / 薬物数 : 4 - (DrugBank : 1) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
2'-O-(2-methoxyethyl)-D-ribose antisense oligonucleotide targeting
   IONIS PHARMACEUTICALS, INC.
      2021   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-IT   Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
2'-O-(2-methoxyethyl)-D-ribose antisense oligonucleotide targeting glial fibrillary acidic protein messenger ribonucleic acid
   Ionis Pharmaceuticals
      2021   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-NL   Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
   Ionis Pharmaceuticals, Inc
      -   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-GB   Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
ION373
   IONIS PHARMACEUTICALS, INC.
      2021   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-IT   Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
   Ionis Pharmaceuticals
      2021   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-NL   Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
   Ionis Pharmaceuticals, Inc
      -   Phase 1;Phase 2;Phase 3   EUCTR2020-000976-40-GB   Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Zilganersen
   Ionis Pharmaceuticals, Inc.
      2021   Phase 3   NCT04849741   Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States