131. アレキサンダー病 Disease details / Clinical trials / Drug dev / DR info /
臨床試験数 : 4 / 薬物数 : 4 - (DrugBank : 1) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
2'-O-(2-methoxyethyl)-D-ribose antisense oligonucleotide targeting
IONIS PHARMACEUTICALS, INC.
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-IT Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
2'-O-(2-methoxyethyl)-D-ribose antisense oligonucleotide targeting glial fibrillary acidic protein messenger ribonucleic acid
Ionis Pharmaceuticals
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-NL Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals, Inc
- Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-GB Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
ION373
IONIS PHARMACEUTICALS, INC.
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-IT Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-NL Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals, Inc
- Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-GB Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Zilganersen
Ionis Pharmaceuticals, Inc.
2021 Phase 3 NCT04849741 Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
IONIS PHARMACEUTICALS, INC.
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-IT Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
2'-O-(2-methoxyethyl)-D-ribose antisense oligonucleotide targeting glial fibrillary acidic protein messenger ribonucleic acid
Ionis Pharmaceuticals
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-NL Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals, Inc
- Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-GB Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
ION373
IONIS PHARMACEUTICALS, INC.
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-IT Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals
2021 Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-NL Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Ionis Pharmaceuticals, Inc
- Phase 1;Phase 2;Phase 3 EUCTR2020-000976-40-GB Argentina;Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States
Zilganersen
Ionis Pharmaceuticals, Inc.
2021 Phase 3 NCT04849741 Australia;Canada;Israel;Italy;Japan;Netherlands;United Kingdom;United States