169. メンケス病 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 7 / 薬物数 : 7 - (DrugBank : 4) / 標的遺伝子数 : 9 - 標的パスウェイ数 : 16

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Copper
   Hamamatsu University School of Medicine
      2014   -   JPRN-UMIN000030626   Japan
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Copper histidinate
   Sentynl Therapeutics, Inc.
      2019   -   NCT04074512   -
Copper histidine
   Cyprium Therapeutics, Inc.
      2009   Phase 3   NCT00811785   United States
   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
      1990   Phase 1/Phase 2   NCT00001262   United States
Diethyldithiocarbamate
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Droxidopa
   Stephen G. Kaler, MD
      2021   Phase 1/Phase 2   NCT04977388   United States
Histidine
   Hamamatsu University School of Medicine
      2014   -   JPRN-UMIN000030626   Japan
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Long term follow-UP
   Cyprium Therapeutics, Inc.
      2019   -   NCT04337684   United States