202. スミス・マギニス症候群 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 9 / 薬物数 : 8 - (DrugBank : 3) / 標的遺伝子数 : 3 - 標的パスウェイ数 : 4

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Acylated and unacylated ghrelin dosages
   University Hospital, Toulouse
      2021   -   NCT04768803   France
Enviro-light artificial light BOX
   Oregon Health and Science University
      1998   -   NCT00691574   United States
Hourly dosing OF THE nychtemeral secretion OF melatonin
   Hôpital le Vinatier
      2018   -   NCT03492970   France
Melatonin
   Oregon Health and Science University
      1998   -   NCT00691574   United States
Melatonin CR
   National Human Genome Research Institute (NHGRI)
      2007   Phase 1   NCT00506259   United States
RM-493
   Rhythm Pharmaceuticals, Inc.
      2020   Phase 2   EUCTR2017-000387-14-GR   Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
      2017   Phase 2   EUCTR2017-000387-14-GB   Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
      -   Phase 2   EUCTR2017-000387-14-FR   Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Setmelanotide
   Rhythm Pharmaceuticals, Inc.
      2020   Phase 2   EUCTR2017-000387-14-GR   Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
      2017   Phase 2   EUCTR2017-000387-14-GB   Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
      -   Phase 2   EUCTR2017-000387-14-FR   Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Tasimelteon
   Vanda Pharmaceuticals
      2016   Phase 1   NCT02776215   United States
      2015   Phase 2/Phase 3   NCT02231008   United States