211. 左心低形成症候群 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 23 / 薬物数 : 29 - (DrugBank : 11) / 標的遺伝子数 : 5 - 標的パスウェイ数 : 13
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
ALLO-hmscs
Longeveron Inc.
2015 Phase 1 NCT02398604 United States
Ambrisentan
Kevin Hill
2015 Phase 2 NCT02080637 United States
Autologous (self) mononuclear cells derived from umbilical cord blood
Timothy J Nelson, MD, PhD
2019 Phase 2 NCT03779711 United States
Autologous CELL-based delivery
Timothy J Nelson, MD, PhD
2013 Phase 1 NCT01883076 United States
Autologous umbilical cord blood
Michael Cotten
2011 Phase 1 NCT01445041 United States
Bosentan
Rigshospitalet, Denmark
2011 Phase 2 NCT01292551 Denmark;Sweden
C-KIT+ cells
Joshua M Hare
2019 Phase 1 NCT03406884 United States
Cardiac progenitor cell infusion
Okayama University
2013 Phase 2 NCT01829750 Japan
Curosurf
University of Michigan
2020 Phase 1 NCT04181255 United States
Erythropoetin
Baylor College of Medicine
2006 Phase 1/Phase 2 NCT00513240 United States
Lomecel-B medicinal signaling cells
Longeveron Inc.
2021 Phase 2 NCT04925024 United States
Longeveron mesenchymal stem cells
Longeveron Inc.
2018 Phase 1/Phase 2 NCT03525418 United States
Maternal hyperoxygenation
Beijing Anzhen Hospital
2016 - NCT03147014 China
The Hospital for Sick Children
2018 Phase 1/Phase 2 NCT03136835 Canada
Methylprednisolone sodium succinate
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
Metyyliprednisoloninatriumsuksinaatti
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
MPC
Boston Children's Hospital
2017 Phase 1/Phase 2 NCT03079401 United States
Nitrogen
Institutional Review Board of Kagoshima University
2015 - JPRN-UMIN000017311 Japan
Normal saline
Baylor College of Medicine
2006 Phase 1/Phase 2 NCT00513240 United States
O2, GAS FOR medical purposes
Universitätsklinikum Erlangen
2022 Phase 3 EUCTR2022-000608-36-DE Germany
Oxandrolone
Carelon Research
2019 Phase 1/Phase 2 NCT04090697 Canada;United States
Oxygen, medical GAS
Universitätsklinikum Erlangen
2022 Phase 3 EUCTR2022-000608-36-DE Germany
Rexlemestrocel-L
Boston Children's Hospital
2017 Phase 1/Phase 2 NCT03079401 United States
Sham
University of Michigan
2020 Phase 1 NCT04181255 United States
Sildenafil
Children's Hospital of Philadelphia
2007 Phase 2 NCT00507819 United States
SOLU-medrol
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
Stage II surgical repair
Timothy J Nelson, MD, PhD
2019 Phase 2 NCT03779711 United States
Tracleer
Lars Søndergaard
2010 - EUCTR2010-022389-28-DK Denmark
Ventrix BIO extracellular matrix
Emory University
2025 Phase 1 NCT06461676 United States
Vitamin C
University of Michigan
2009 - NCT00974025 United States
Longeveron Inc.
2015 Phase 1 NCT02398604 United States
Ambrisentan
Kevin Hill
2015 Phase 2 NCT02080637 United States
Autologous (self) mononuclear cells derived from umbilical cord blood
Timothy J Nelson, MD, PhD
2019 Phase 2 NCT03779711 United States
Autologous CELL-based delivery
Timothy J Nelson, MD, PhD
2013 Phase 1 NCT01883076 United States
Autologous umbilical cord blood
Michael Cotten
2011 Phase 1 NCT01445041 United States
Bosentan
Rigshospitalet, Denmark
2011 Phase 2 NCT01292551 Denmark;Sweden
C-KIT+ cells
Joshua M Hare
2019 Phase 1 NCT03406884 United States
Cardiac progenitor cell infusion
Okayama University
2013 Phase 2 NCT01829750 Japan
Curosurf
University of Michigan
2020 Phase 1 NCT04181255 United States
Erythropoetin
Baylor College of Medicine
2006 Phase 1/Phase 2 NCT00513240 United States
Lomecel-B medicinal signaling cells
Longeveron Inc.
2021 Phase 2 NCT04925024 United States
Longeveron mesenchymal stem cells
Longeveron Inc.
2018 Phase 1/Phase 2 NCT03525418 United States
Maternal hyperoxygenation
Beijing Anzhen Hospital
2016 - NCT03147014 China
The Hospital for Sick Children
2018 Phase 1/Phase 2 NCT03136835 Canada
Methylprednisolone sodium succinate
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
Metyyliprednisoloninatriumsuksinaatti
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
MPC
Boston Children's Hospital
2017 Phase 1/Phase 2 NCT03079401 United States
Nitrogen
Institutional Review Board of Kagoshima University
2015 - JPRN-UMIN000017311 Japan
Normal saline
Baylor College of Medicine
2006 Phase 1/Phase 2 NCT00513240 United States
O2, GAS FOR medical purposes
Universitätsklinikum Erlangen
2022 Phase 3 EUCTR2022-000608-36-DE Germany
Oxandrolone
Carelon Research
2019 Phase 1/Phase 2 NCT04090697 Canada;United States
Oxygen, medical GAS
Universitätsklinikum Erlangen
2022 Phase 3 EUCTR2022-000608-36-DE Germany
Rexlemestrocel-L
Boston Children's Hospital
2017 Phase 1/Phase 2 NCT03079401 United States
Sham
University of Michigan
2020 Phase 1 NCT04181255 United States
Sildenafil
Children's Hospital of Philadelphia
2007 Phase 2 NCT00507819 United States
SOLU-medrol
Pertti Suominen
2009 - EUCTR2008-007413-76-FI Finland
Stage II surgical repair
Timothy J Nelson, MD, PhD
2019 Phase 2 NCT03779711 United States
Tracleer
Lars Søndergaard
2010 - EUCTR2010-022389-28-DK Denmark
Ventrix BIO extracellular matrix
Emory University
2025 Phase 1 NCT06461676 United States
Vitamin C
University of Michigan
2009 - NCT00974025 United States