211. 左心低形成症候群 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 23 / 薬物数 : 29 - (DrugBank : 11) / 標的遺伝子数 : 5 - 標的パスウェイ数 : 13

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
ALLO-hmscs
   Longeveron Inc.
      2015   Phase 1   NCT02398604   United States
Ambrisentan
   Kevin Hill
      2015   Phase 2   NCT02080637   United States
Autologous (self) mononuclear cells derived from umbilical cord blood
   Timothy J Nelson, MD, PhD
      2019   Phase 2   NCT03779711   United States
Autologous CELL-based delivery
   Timothy J Nelson, MD, PhD
      2013   Phase 1   NCT01883076   United States
Autologous umbilical cord blood
   Michael Cotten
      2011   Phase 1   NCT01445041   United States
Bosentan
   Rigshospitalet, Denmark
      2011   Phase 2   NCT01292551   Denmark;Sweden
C-KIT+ cells
   Joshua M Hare
      2019   Phase 1   NCT03406884   United States
Cardiac progenitor cell infusion
   Okayama University
      2013   Phase 2   NCT01829750   Japan
Curosurf
   University of Michigan
      2020   Phase 1   NCT04181255   United States
Erythropoetin
   Baylor College of Medicine
      2006   Phase 1/Phase 2   NCT00513240   United States
Lomecel-B medicinal signaling cells
   Longeveron Inc.
      2021   Phase 2   NCT04925024   United States
Longeveron mesenchymal stem cells
   Longeveron Inc.
      2018   Phase 1/Phase 2   NCT03525418   United States
Maternal hyperoxygenation
   Beijing Anzhen Hospital
      2016   -   NCT03147014   China
   The Hospital for Sick Children
      2018   Phase 1/Phase 2   NCT03136835   Canada
Methylprednisolone sodium succinate
   Pertti Suominen
      2009   -   EUCTR2008-007413-76-FI   Finland
Metyyliprednisoloninatriumsuksinaatti
   Pertti Suominen
      2009   -   EUCTR2008-007413-76-FI   Finland
MPC
   Boston Children's Hospital
      2017   Phase 1/Phase 2   NCT03079401   United States
Nitrogen
   Institutional Review Board of Kagoshima University
      2015   -   JPRN-UMIN000017311   Japan
Normal saline
   Baylor College of Medicine
      2006   Phase 1/Phase 2   NCT00513240   United States
O2, GAS FOR medical purposes
   Universitätsklinikum Erlangen
      2022   Phase 3   EUCTR2022-000608-36-DE   Germany
Oxandrolone
   Carelon Research
      2019   Phase 1/Phase 2   NCT04090697   Canada;United States
Oxygen, medical GAS
   Universitätsklinikum Erlangen
      2022   Phase 3   EUCTR2022-000608-36-DE   Germany
Rexlemestrocel-L
   Boston Children's Hospital
      2017   Phase 1/Phase 2   NCT03079401   United States
Sham
   University of Michigan
      2020   Phase 1   NCT04181255   United States
Sildenafil
   Children's Hospital of Philadelphia
      2007   Phase 2   NCT00507819   United States
SOLU-medrol
   Pertti Suominen
      2009   -   EUCTR2008-007413-76-FI   Finland
Stage II surgical repair
   Timothy J Nelson, MD, PhD
      2019   Phase 2   NCT03779711   United States
Tracleer
   Lars Søndergaard
      2010   -   EUCTR2010-022389-28-DK   Denmark
Ventrix BIO extracellular matrix
   Emory University
      2025   Phase 1   NCT06461676   United States
Vitamin C
   University of Michigan
      2009   -   NCT00974025   United States