227. オスラー病 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 57 / 薬物数 : 60 - (DrugBank : 20) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 151
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Avastin
AZIENDA OSPEDALIERA OSPEDALE POLICLINICO CONSORZIALE
2008 - EUCTR2010-020545-26-IT Italy
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Hospices Civils de Lyon
2017 Phase 3 EUCTR2017-001031-39-FR France
2014 - EUCTR2013-004204-19-FR France
Avastin 25 MG/ML - konzentrat ZUR herstellung einer infusionsloesung
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Bevacizumab
AZIENDA OSPEDALIERA OSPEDALE POLICLINICO CONSORZIALE
2008 - EUCTR2010-020545-26-IT Italy
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Hanny Al-Samkari, MD
2020 Phase 2 NCT04404881 United States
Hospices Civils de Lyon
2017 Phase 3 NCT03227263 France
2017 Phase 3 EUCTR2017-001031-39-FR France
2014 Phase 2/Phase 3 NCT02106520 France
2014 - EUCTR2013-004204-19-FR France
2011 Phase 1 NCT01507480 France
James Gossage
2011 Phase 2 NCT01408030 United States
Medical University of Vienna
2011 Phase 2 NCT01314274 Austria
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Shandong Provincial ENT Hospital
2021 Phase 4 ChiCTR2100043253 China
Stanford University
2014 Phase 4 NCT02389959 United States
University of California, San Diego
2009 Phase 2 NCT01397695 United States
Bevacuzimab spray
University Hospital, Caen
2014 Phase 1/Phase 2 NCT02157987 France
Blood samples
Centre Hospitalier Universitaire Dijon
2018 - NCT03572556 France
Cord blood sampling
Hospices Civils de Lyon
2023 - NCT05632484 France
Cord sampling
Hospices Civils de Lyon
2023 - NCT05632484 France
Dicynone
Asociación HHT España
2017 Phase 2;Phase 4 EUCTR2016-003982-24-ES Spain
Doxycycline hyclate
Unity Health Toronto
2018 Phase 2 NCT03397004 Canada
Emea/H/C/000712
St. Antonius Hospital
2019 Phase 2 EUCTR2019-003585-40-NL Netherlands
Epistaxis charts
Centre Hospitalier Universitaire Dijon
2018 - NCT03572556 France
Estriol
James Gossage
2011 Phase 2 NCT01408030 United States
Etamsylate
Asociación HHT España
2017 Phase 2;Phase 4 EUCTR2016-003982-24-ES Spain
Ferrous sulphate 200MG oral tablet
Imperial College London
2013 - NCT01908543 United Kingdom
Floseal
St. Michael's Hospital, Toronto
2015 - NCT02638012 Canada
Itraconazole
St. Antonius Ziekenhuis
2018 Phase 2 EUCTR2017-003272-31-NL Netherlands
Mupirocin
Hospital Italiano de Buenos Aires
2017 Phase 3 NCT02963129 Argentina
Nacl
Medical University of Vienna
2011 Phase 2 NCT01314274 Austria
Nintedanib
Dr. Romain Lazor
2022 Phase 2 NCT04976036 Switzerland
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Nintedanib 150 MG and 100 MG soft capsules
Hospices Civils de Lyon
2020 Phase 2 NCT03954782 France
Nintédanib
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Octreotide
National Center for Research Resources (NCRR)
1995 Phase 2 NCT00004327 -
Radboudumc
2021 Phase 3 EUCTR2018-004179-11-FR France;Germany;Italy;Netherlands
2019 Phase 3 EUCTR2018-004179-11-NL Netherlands
Octreotide A azione pronta 0,1 MG
RADBOUD UNIVERSITY MEDICAL CENTER
2021 Phase 3 EUCTR2018-004179-11-IT Denmark;France;Germany;Italy;Netherlands;United Kingdom
Octreotide acetate
Radboudumc
2020 Phase 3 EUCTR2018-004179-11-DE France;Germany;Italy;Netherlands;United Kingdom
Octreotide acetato
RADBOUD UNIVERSITY MEDICAL CENTER
2021 Phase 3 EUCTR2018-004179-11-IT Denmark;France;Germany;Italy;Netherlands;United Kingdom
Octreotide LAR
Radboud University
2016 Phase 2 NCT02874326 Netherlands
Ofev
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Packing
St. Michael's Hospital, Toronto
2015 - NCT02638012 Canada
Pazopanib
Cure HHT
2023 Phase 2/Phase 3 NCT03850964 United States
2023 Phase 1/Phase 2 NCT03850730 -
Pegylated interferon alpha2B
Mayo Clinic
2007 Phase 2 NCT00588146 United States
Physiologische kochsalzloesung fresenius - infusionsloesung
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Pomalidomide
The Cleveland Clinic
2015 Phase 1 NCT02287558 United States
Pomalidomide oral product
The Cleveland Clinic
2019 Phase 2 NCT03910244 United States
Propranolol treatment
University Hospital, Bordeaux
2020 Phase 3 NCT04113187 France
Ranibizumab
University of California, San Diego
2011 Phase 1 NCT01406639 United States
RVG 18236
Radboud University Medical Center
2016 Phase 2 EUCTR2016-001340-19-NL Netherlands
Sandostatin LAR 20 MG
Radboud University Medical Center
2016 Phase 2 EUCTR2016-001340-19-NL Netherlands
Sclerotherapy
University of Minnesota
2011 Phase 1/Phase 2 NCT01408732 United States
Sirolimus
Unity Health Toronto
2022 Phase 2 NCT05269849 Canada
Sodium chloride
Hospices Civils de Lyon
2017 Phase 3 NCT03227263 France
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
SOY protein isolate
National Center for Research Resources (NCRR)
1996 Phase 3 NCT00004654 -
Sporanox
St. Antonius Ziekenhuis
2018 Phase 2 EUCTR2017-003272-31-NL Netherlands
Standard care
Mayo Clinic
2007 Phase 2 NCT00588146 United States
Standard treatment
University of Minnesota
2011 Phase 1/Phase 2 NCT01408732 United States
Sterile saline
James Gossage
2011 Phase 2 NCT01408030 United States
SUB16402MIG
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Submucosal bevacizumab
University of California, San Diego
2010 Phase 2 NCT01402531 United States
Tacrolimus
St. Antonius Hospital
2019 Phase 2 EUCTR2019-003585-40-NL Netherlands
Unity Health Toronto
2020 Phase 2 NCT04646356 Canada
Tamoxifen
Rabin Medical Center
2005 Phase 2 NCT00375622 Israel
Thalidomide
IRCCS Policlinico S. Matteo
2011 Phase 2 NCT01485224 Italy
Northport Veterans Affairs Medical Center
2006 Phase 2 NCT00389935 United States
Thalidomide celgene*28CPS 50MG
OSPEDALE POLICLINICO S. MATTEO
2011 Phase 2 EUCTR2011-004096-36-IT Italy
Timolol alcon 0.5% collyre
Hospices Civils de Lyon
2015 Phase 2 EUCTR2015-000385-55-FR France
Timolol GEL
Washington University School of Medicine
2019 Phase 2 NCT04139018 United States
Timolol maleate
Hospices Civils de Lyon
2015 Phase 2 EUCTR2015-000385-55-FR France
Timolol nasal spray
Hospices Civils de Lyon
2015 Phase 2 NCT02484716 France
Topical timolol maleate
Unity Health Toronto
2013 - NCT01752049 Canada
Tranexamic acid
James Gossage
2011 Phase 2 NCT01408030 United States
University Hospital, Saarland
2002 Phase 3 NCT01031992 Germany
VAD044 part I
Vaderis Therapeutics AG
2022 Phase 1/Phase 2 NCT05406362 Belgium;Canada;France;Italy;Netherlands;Spain;United States
VAD044 part II
Vaderis Therapeutics AG
2022 Phase 1/Phase 2 NCT05406362 Belgium;Canada;France;Italy;Netherlands;Spain;United States
VIT D
St. Paul's Hospital, Canada
2018 Phase 2 NCT03981562 Canada
AZIENDA OSPEDALIERA OSPEDALE POLICLINICO CONSORZIALE
2008 - EUCTR2010-020545-26-IT Italy
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Hospices Civils de Lyon
2017 Phase 3 EUCTR2017-001031-39-FR France
2014 - EUCTR2013-004204-19-FR France
Avastin 25 MG/ML - konzentrat ZUR herstellung einer infusionsloesung
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Bevacizumab
AZIENDA OSPEDALIERA OSPEDALE POLICLINICO CONSORZIALE
2008 - EUCTR2010-020545-26-IT Italy
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Hanny Al-Samkari, MD
2020 Phase 2 NCT04404881 United States
Hospices Civils de Lyon
2017 Phase 3 NCT03227263 France
2017 Phase 3 EUCTR2017-001031-39-FR France
2014 Phase 2/Phase 3 NCT02106520 France
2014 - EUCTR2013-004204-19-FR France
2011 Phase 1 NCT01507480 France
James Gossage
2011 Phase 2 NCT01408030 United States
Medical University of Vienna
2011 Phase 2 NCT01314274 Austria
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Shandong Provincial ENT Hospital
2021 Phase 4 ChiCTR2100043253 China
Stanford University
2014 Phase 4 NCT02389959 United States
University of California, San Diego
2009 Phase 2 NCT01397695 United States
Bevacuzimab spray
University Hospital, Caen
2014 Phase 1/Phase 2 NCT02157987 France
Blood samples
Centre Hospitalier Universitaire Dijon
2018 - NCT03572556 France
Cord blood sampling
Hospices Civils de Lyon
2023 - NCT05632484 France
Cord sampling
Hospices Civils de Lyon
2023 - NCT05632484 France
Dicynone
Asociación HHT España
2017 Phase 2;Phase 4 EUCTR2016-003982-24-ES Spain
Doxycycline hyclate
Unity Health Toronto
2018 Phase 2 NCT03397004 Canada
Emea/H/C/000712
St. Antonius Hospital
2019 Phase 2 EUCTR2019-003585-40-NL Netherlands
Epistaxis charts
Centre Hospitalier Universitaire Dijon
2018 - NCT03572556 France
Estriol
James Gossage
2011 Phase 2 NCT01408030 United States
Etamsylate
Asociación HHT España
2017 Phase 2;Phase 4 EUCTR2016-003982-24-ES Spain
Ferrous sulphate 200MG oral tablet
Imperial College London
2013 - NCT01908543 United Kingdom
Floseal
St. Michael's Hospital, Toronto
2015 - NCT02638012 Canada
Itraconazole
St. Antonius Ziekenhuis
2018 Phase 2 EUCTR2017-003272-31-NL Netherlands
Mupirocin
Hospital Italiano de Buenos Aires
2017 Phase 3 NCT02963129 Argentina
Nacl
Medical University of Vienna
2011 Phase 2 NCT01314274 Austria
Nintedanib
Dr. Romain Lazor
2022 Phase 2 NCT04976036 Switzerland
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Nintedanib 150 MG and 100 MG soft capsules
Hospices Civils de Lyon
2020 Phase 2 NCT03954782 France
Nintédanib
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Octreotide
National Center for Research Resources (NCRR)
1995 Phase 2 NCT00004327 -
Radboudumc
2021 Phase 3 EUCTR2018-004179-11-FR France;Germany;Italy;Netherlands
2019 Phase 3 EUCTR2018-004179-11-NL Netherlands
Octreotide A azione pronta 0,1 MG
RADBOUD UNIVERSITY MEDICAL CENTER
2021 Phase 3 EUCTR2018-004179-11-IT Denmark;France;Germany;Italy;Netherlands;United Kingdom
Octreotide acetate
Radboudumc
2020 Phase 3 EUCTR2018-004179-11-DE France;Germany;Italy;Netherlands;United Kingdom
Octreotide acetato
RADBOUD UNIVERSITY MEDICAL CENTER
2021 Phase 3 EUCTR2018-004179-11-IT Denmark;France;Germany;Italy;Netherlands;United Kingdom
Octreotide LAR
Radboud University
2016 Phase 2 NCT02874326 Netherlands
Ofev
Hospices Civils de Lyon
2019 Phase 2 EUCTR2019-002593-31-FR France
Packing
St. Michael's Hospital, Toronto
2015 - NCT02638012 Canada
Pazopanib
Cure HHT
2023 Phase 2/Phase 3 NCT03850964 United States
2023 Phase 1/Phase 2 NCT03850730 -
Pegylated interferon alpha2B
Mayo Clinic
2007 Phase 2 NCT00588146 United States
Physiologische kochsalzloesung fresenius - infusionsloesung
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
Pomalidomide
The Cleveland Clinic
2015 Phase 1 NCT02287558 United States
Pomalidomide oral product
The Cleveland Clinic
2019 Phase 2 NCT03910244 United States
Propranolol treatment
University Hospital, Bordeaux
2020 Phase 3 NCT04113187 France
Ranibizumab
University of California, San Diego
2011 Phase 1 NCT01406639 United States
RVG 18236
Radboud University Medical Center
2016 Phase 2 EUCTR2016-001340-19-NL Netherlands
Sandostatin LAR 20 MG
Radboud University Medical Center
2016 Phase 2 EUCTR2016-001340-19-NL Netherlands
Sclerotherapy
University of Minnesota
2011 Phase 1/Phase 2 NCT01408732 United States
Sirolimus
Unity Health Toronto
2022 Phase 2 NCT05269849 Canada
Sodium chloride
Hospices Civils de Lyon
2017 Phase 3 NCT03227263 France
Medizinische Universität Wien,Univ.Klinik f.Hals-, Nasen- und Ohrenkrankheiten
2010 - EUCTR2009-018049-19-AT Austria
SOY protein isolate
National Center for Research Resources (NCRR)
1996 Phase 3 NCT00004654 -
Sporanox
St. Antonius Ziekenhuis
2018 Phase 2 EUCTR2017-003272-31-NL Netherlands
Standard care
Mayo Clinic
2007 Phase 2 NCT00588146 United States
Standard treatment
University of Minnesota
2011 Phase 1/Phase 2 NCT01408732 United States
Sterile saline
James Gossage
2011 Phase 2 NCT01408030 United States
SUB16402MIG
HOSPICES CIVILS DE LYON
2009 - EUCTR2008-006755-44-FR France
Submucosal bevacizumab
University of California, San Diego
2010 Phase 2 NCT01402531 United States
Tacrolimus
St. Antonius Hospital
2019 Phase 2 EUCTR2019-003585-40-NL Netherlands
Unity Health Toronto
2020 Phase 2 NCT04646356 Canada
Tamoxifen
Rabin Medical Center
2005 Phase 2 NCT00375622 Israel
Thalidomide
IRCCS Policlinico S. Matteo
2011 Phase 2 NCT01485224 Italy
Northport Veterans Affairs Medical Center
2006 Phase 2 NCT00389935 United States
Thalidomide celgene*28CPS 50MG
OSPEDALE POLICLINICO S. MATTEO
2011 Phase 2 EUCTR2011-004096-36-IT Italy
Timolol alcon 0.5% collyre
Hospices Civils de Lyon
2015 Phase 2 EUCTR2015-000385-55-FR France
Timolol GEL
Washington University School of Medicine
2019 Phase 2 NCT04139018 United States
Timolol maleate
Hospices Civils de Lyon
2015 Phase 2 EUCTR2015-000385-55-FR France
Timolol nasal spray
Hospices Civils de Lyon
2015 Phase 2 NCT02484716 France
Topical timolol maleate
Unity Health Toronto
2013 - NCT01752049 Canada
Tranexamic acid
James Gossage
2011 Phase 2 NCT01408030 United States
University Hospital, Saarland
2002 Phase 3 NCT01031992 Germany
VAD044 part I
Vaderis Therapeutics AG
2022 Phase 1/Phase 2 NCT05406362 Belgium;Canada;France;Italy;Netherlands;Spain;United States
VAD044 part II
Vaderis Therapeutics AG
2022 Phase 1/Phase 2 NCT05406362 Belgium;Canada;France;Italy;Netherlands;Spain;United States
VIT D
St. Paul's Hospital, Canada
2018 Phase 2 NCT03981562 Canada