244. メープルシロップ尿症 Disease details / Clinical trials / Drug dev / DR info /


臨床試験数 : 5 / 薬物数 : 12 - (DrugBank : 2) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Isoleucine
   Meta Healthcare Ltd
      2024   -   NCT06581991   -
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Phenylbutyrate
   Brendan Lee
      2013   Phase 2/Phase 3   NCT01529060   United States
PKU express plus
   Vitaflo International, Ltd
      2021   -   NCT05051657   United Kingdom
Valine
   Meta Healthcare Ltd
      2024   -   NCT06581991   -