326. 大理石骨病 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 18 / 薬物数 : 37 - (DrugBank : 16) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 93
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Actimmune
Indiana University
2016 Phase 2 NCT02584608 United States
Actimmune registry
InterMune
2002 - NCT00043329 United States
Alemtuzumab
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
AP1903
Bellicum Pharmaceuticals, Inc.
2017 Phase 1;Phase 2 EUCTR2016-003226-16-IT Italy
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
2014 Phase 1;Phase 2 EUCTR2014-000584-41-IT Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
BPX-501 cells
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
2014 Phase 1;Phase 2 EUCTR2014-000584-41-IT Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
BPX-501 T cells
Bellicum Pharmaceuticals
2014 Phase 1/Phase 2 NCT02065869 Germany;Italy;Spain;United Kingdom;United States
Busulfan
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Calcitriol
FDA Office of Orphan Products Development
1999 Phase 3 NCT00004402 -
Campath, busulfan, clofarabine
Masonic Cancer Center, University of Minnesota
2007 Phase 2 NCT00638820 United States
Campath-1H
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
CD34+ enriched, T cell depleted donor stem cell product
Christopher Dvorak
2010 - NCT01200017 United States
Cyclophosphamide
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Cyclosporin
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Fludarabine
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Fludarabine monophosphate
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Hematopoetic stem cell transplantation
University of Pittsburgh
2012 - NCT03333200 United States
Horse ANTI-thymocyte globulin
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
IMD preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Interferon gamma
FDA Office of Orphan Products Development
1999 Phase 3 NCT00004402 -
Interferon gamma-1B
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center
2016 Phase 2 NCT02666768 United States
Marrow graft transplantation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Methotrexate
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Miltenyi biotec clinimacs
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Osteopetrosis haploidentical only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Palliative care
University of Pittsburgh
2012 - NCT03333200 United States
Rabbit ANTI-thymocyte globulin
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Rhpth
University of Chicago
2003 Phase 1 NCT00145886 United States
Rimiducid
Bellicum Pharmaceuticals
2014 Phase 1/Phase 2 NCT02065869 Germany;Italy;Spain;United Kingdom;United States
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
Rivogenlecleucel
Bellicum Pharmaceuticals, Inc.
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
Rivogenleucleucel
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
Stem cell or umbilical cord blood transplantation
Masonic Cancer Center, University of Minnesota
2007 Phase 2 NCT00638820 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Systemic chemotherapy and antibodies
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Thymoglobulin
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Total lymphoid irradiation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
2007 Phase 2 NCT00638820 United States
Umbilical cord blood transplantation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Indiana University
2016 Phase 2 NCT02584608 United States
Actimmune registry
InterMune
2002 - NCT00043329 United States
Alemtuzumab
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
AP1903
Bellicum Pharmaceuticals, Inc.
2017 Phase 1;Phase 2 EUCTR2016-003226-16-IT Italy
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
2014 Phase 1;Phase 2 EUCTR2014-000584-41-IT Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
BPX-501 cells
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
2014 Phase 1;Phase 2 EUCTR2014-000584-41-IT Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
BPX-501 T cells
Bellicum Pharmaceuticals
2014 Phase 1/Phase 2 NCT02065869 Germany;Italy;Spain;United Kingdom;United States
Busulfan
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Calcitriol
FDA Office of Orphan Products Development
1999 Phase 3 NCT00004402 -
Campath, busulfan, clofarabine
Masonic Cancer Center, University of Minnesota
2007 Phase 2 NCT00638820 United States
Campath-1H
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
CD34+ enriched, T cell depleted donor stem cell product
Christopher Dvorak
2010 - NCT01200017 United States
Cyclophosphamide
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Cyclosporin
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Fludarabine
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Fludarabine monophosphate
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Hematopoetic stem cell transplantation
University of Pittsburgh
2012 - NCT03333200 United States
Horse ANTI-thymocyte globulin
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
IMD preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Interferon gamma
FDA Office of Orphan Products Development
1999 Phase 3 NCT00004402 -
Interferon gamma-1B
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center
2016 Phase 2 NCT02666768 United States
Marrow graft transplantation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
Methotrexate
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Miltenyi biotec clinimacs
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Osteopetrosis haploidentical only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Palliative care
University of Pittsburgh
2012 - NCT03333200 United States
Rabbit ANTI-thymocyte globulin
Columbia University
2002 Phase 2/Phase 3 NCT01019876 United States
Rhpth
University of Chicago
2003 Phase 1 NCT00145886 United States
Rimiducid
Bellicum Pharmaceuticals
2014 Phase 1/Phase 2 NCT02065869 Germany;Italy;Spain;United Kingdom;United States
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
Rivogenlecleucel
Bellicum Pharmaceuticals, Inc.
- Phase 2 EUCTR2014-000584-41-GB Italy;Spain;United Kingdom
Rivogenleucleucel
Bellicum Pharmaceuticals, Inc.
2017 Phase 2 EUCTR2014-000584-41-ES Italy;Spain;United Kingdom
Stem cell or umbilical cord blood transplantation
Masonic Cancer Center, University of Minnesota
2007 Phase 2 NCT00638820 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Systemic chemotherapy and antibodies
St. Jude Children's Research Hospital
2004 - NCT00145587 United States
Thymoglobulin
Tehran University of Medical Sciences
2009 Phase 2/Phase 3 NCT01087398 Iran, Islamic Republic of
Total lymphoid irradiation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States
2007 Phase 2 NCT00638820 United States
Umbilical cord blood transplantation
Masonic Cancer Center, University of Minnesota
2008 Phase 2/Phase 3 NCT00775931 United States