344. 極長鎖アシル-CoA 脱水素酵素欠損症 Disease details / Clinical trials / Drug dev / DR info /

臨床試験数 : 6 / 薬物数 : 10 - (DrugBank : 2) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 10

薬物、開発者（Primary Sponsor）、臨床試験情報（症例登録開始年（Enrollment year）、フェーズ、ID、実施国）
Bezafibrate
   Rigshospitalet, Denmark
      2009   Phase 2   NCT00983788   Denmark
Exercise
   University Medical Center Groningen
      2016   -   NCT03531554   Netherlands
Glycerol/saline
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Hyperinsulinemic euglycemic clamp
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Intralipid/heparin
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Ketone ester drink
   University Medical Center Groningen
      2016   -   NCT03531554   Netherlands
Magnetic resonance imaging
   University Medical Center Groningen
      2016   -   NCT03531554   Netherlands
Muscle biopsy
   University Medical Center Groningen
      2016   -   NCT03531554   Netherlands
Nutritional ketone supplement
   Oregon Health and Science University
      2022   Early Phase 1   NCT05411835   United States
UX007
   Ultragenyx Pharmaceutical Inc
      2014   Phase 2   NCT02214160   United Kingdom;United States
      2014   Phase 2   NCT01886378   United Kingdom;United States