Drug Description in Trials / DrugBank / KEGG DRUG /
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| No. | 薬物名(臨床試験情報から抽出) | DrugBank | KEGG DRUG | KEGG GENES | KEGG PATHWAY | 指定難病告示番号 |
|---|---|---|---|---|---|---|
| 1 | Blood draw for the laboratory assessment | - | - | - | - | 1件: 303 303 |
| 2 | Lentiviral vector containing MYO7A gene | - | - | - | - | 2件: 90 90, 303 |
| 3 | Lentiviral vector containing the human MY07A gene | - | - | - | - | 2件: 90 90, 303 |
| 4 | NPI-001 | - | - | - | - | 2件: 90 90, 303 |
| 5 | NT-501 | - | - | - | - | 2件: 90 90, 303 |
| 6 | Other: Sham-procedure | - | - | - | - | 2件: 90 90, 303 |
| 7 | Other: Sham-procedure (dose cohort 1&2 only) | - | - | - | - | 2件: 90 90, 303 |
| 8 | QR-421a | - | - | - | - | 2件: 90 90, 303 |
| 9 | RNA antisense oligonucleotide for intravitreal injection | - | - | - | - | 2件: 90 90, 303 |
| 10 | SAR421869 | - | - | - | - | 2件: 90 90, 303 |
| 11 | Sham | - | - | - | - | 3件: 90 90, 211, 303 |
| 12 | UshStat | - | - | - | - | 2件: 90 90, 303 |
| 13 | UshStat (SAR421869) | - | - | - | - | 2件: 90 90, 303 |