111. 先天性ミオパチー Congenital myopathy Clinical trials / Disease details
臨床試験数 : 11 / 薬物数 : 17 - (DrugBank : 5) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 9
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT02035501 (ClinicalTrials.gov) | January 2014 | 2/7/2013 | Treatment of TNNT1-Myopathy With L-Tyrosine. | Treatment of TNNT1-Myopathy With L-Tyrosine. A Double-blind, Placebo-controlled Crossover Trial. | Nemaline Myopathy | Drug: L-Tyrosine;Drug: Placebo | Hadassah Medical Organization | NULL | Enrolling by invitation | N/A | 20 Years | Both | 10 | Phase 2 | Israel |