19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details
臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04958070 (ClinicalTrials.gov) | October 26, 2021 | 1/7/2021 | The Intensively Follow-up Examinations for Asymptomatic MPS I Infants in Taiwan | The Intensively Follow-up Examinations for Asymptomatic MPS I Infants From Nationwide Newborn Screening Program for Mucopolysaccharidoses in Taiwan. | MPS I | Other: MPS I | Mackay Memorial Hospital | Sanofi Taiwan Co. Ltd | Not yet recruiting | 3 Years | 8 Years | All | 20 | Taiwan |