284. ダイアモンド・ブラックファン貧血 Diamond-Blackfan anemia Clinical trials / Disease details
臨床試験数 : 37 / 薬物数 : 110 - (DrugBank : 34) / 標的遺伝子数 : 23 - 標的パスウェイ数 : 124
| No. | TrialID | Date_ enrollment  | Date_ registration  | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor  | Secondary_ sponsor  | Recruitment_ Status  | Inclusion_ agemin  | Inclusion_ agemax  | Inclusion_ gender  | Target_ size  | Phase | Countries | 
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04269889 (ClinicalTrials.gov)  | December 1, 2020 | 13/2/2020 | Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag | Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag | Anemia, Diamond-Blackfan | Drug: Eltrombopag | National Heart, Lung, and Blood Institute (NHLBI) | NULL | Recruiting | 2 Years | N/A | All | 30 | Phase 1/Phase 2 | United States |