Retrovirus-mediated gene transfer ( DrugBank: - )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
65	原発性免疫不全症候群	2

65. 原発性免疫不全症候群

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臨床試験数 : 482 /  薬物数 : 653 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 212

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01410825 (ClinicalTrials.gov)	July 2011	4/8/2011	Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome	Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome	Wiskott-Aldrich Syndrome	Biological: Retrovirus-mediated gene transfer	David Williams	NULL	Active, not recruiting	3 Months	35 Years	Male	5	Phase 1/Phase 2	United States
2	NCT01129544 (ClinicalTrials.gov)	April 2010	21/5/2010	Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector	Multi-institutional Phase I/II Trial Evaluating the Treatment of SCID-X1 Patients With Retrovirus-mediated Gene Transfer	Severe Combined Immunodeficiency	Biological: Gene transfer	David Williams	Boston Children's Hospital;Children's Hospital Medical Center, Cincinnati;University of California, Los Angeles	Active, not recruiting	N/A	N/A	Male	8	Phase 1/Phase 2	United States