Elapegademase-lvlr    (DrugBank: Elapegademase, Elapegademase-lvlr)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群1

65. 原発性免疫不全症候群 [臨床試験数:413,薬物数:581(DrugBank:97),標的遺伝子数:68,標的パスウェイ数:202
Searched query = "Primary immunodeficiency", "X-SCID", "Reticular dysgenesis", "Adenosine deaminase deficiency", "Omenn syndrome", "Purine nucleoside phosphorylase def ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
1 / 413 trial found
No.TrialIDDate_
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Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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Inclusion_
agemin
Inclusion_
agemax
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PhaseCountries
1NCT03878069
(ClinicalTrials.gov)
June 25, 201912/3/2019Registry Study of Revcovi Treatment in Patients With ADA-SCIDSingle Arm, Open-Label, Multicenter, Registry Study of Revcovi (Elapegademase-lvlr) Treatment in ADA-SCID Patients Requiring Enzyme Replacement TherapyAdenosine Deaminase Deficiency;Severe Combined ImmunodeficiencyBiological: elapegademase-lvlrLeadiant Biosciences, Inc.NULLRecruitingN/A65 YearsAll20United States