DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
164. 眼皮膚白皮症
Oculocutaneous albinism
Clinical trials
/
Disease details
臨床試験数
:
15
/
薬物数
:
54
- (
DrugBank
:
34
) /
標的遺伝子数
:
35
-
標的パスウェイ数
:
141
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TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT01821781
(
ClinicalTrials.gov
)
March 2013
19/3/2013
Immune Disorder HSCT Protocol
A Study of Hematopoietic Stem Cell Transplantation (HSCT) in Immune Function Disorders Using a Reduced Intensity Preparatory Regime
A Study of Hematopoietic Stem Cell Transplantation (HSCT) in Immune Function Disorders Using a Reduc ...
Immune Deficiency Disorders;Severe Combined Immunodeficiency;Chronic Granulomatous Disease;X-linked Agammaglobulinemia;Wiskott-Aldrich Syndrome;Hyper-IgM;DiGeorge Syndrome;Chediak-Higashi Syndrome;Common Variable Immune Deficiency;Immune Dysregulatory Disorders;Hemophagocytic Lymphohistiocytosis;IPEX;Autoimmune Lymphoproliferative Syndrome;X-linked Lymphoproliferative Syndrome
Immune Deficiency Disorders;Severe Combined Immunodeficiency;Chronic Granulomatous Disease;X-linked ...
Drug:
Transplant preparative regimen of alemtuzumab, fludarabine,
thiotepa
, and melphalan
Washington University School of Medicine
NULL
Recruiting
N/A
21 Years
All
20
Phase 2
United States