19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01415427 (ClinicalTrials.gov)	July 2011	8/8/2011	Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA ...	A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 1 ...	Mucopolysaccharidosis IV A;Morquio A Syndrome;MPS IVA	Drug: BMN 110 - Weekly;Drug: BMN 110 - Every Other Week	BioMarin Pharmaceutical	NULL	Completed	5 Years	N/A	All	173	Phase 3	United States;Argentina;Brazil;Canada;Colombia;Denmark;France;Germany;Italy;Japan;Korea, Republic of ...

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