A Study of BIIB067 When Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Dismutase 1 Mutation A Study of BIIB067 When Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Di ...
A Phase 3 Randomized, Placebo-Controlled Trial With a Longitudinal Natural History Run-In and Open-Label Extension to Evaluate BIIB067 Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Dismutase 1 Mutation A Phase 3 Randomized, Placebo-Controlled Trial With a Longitudinal Natural History Run-In and Open-L ...
Amyotrophic Lateral Sclerosis Associated With a SOD1 Gene Mutation