DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
251. 尿素サイクル異常症
Urea cycle disorder
Clinical trials
/
Disease details
臨床試験数
:
54
/
薬物数
:
61
- (
DrugBank
:
15
) /
標的遺伝子数
:
3
-
標的パスウェイ数
:
28
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TrialID
Date_
enrollment
Date_
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Public_title
Scientific_title
Condition
Intervention
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sponsor
Secondary_
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Status
Inclusion_
agemin
Inclusion_
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Phase
Countries
1
JPRN-jRCTs041190055
24/07/2019
24/07/2019
Carglumic Acid
Administration for OTC Deficienscy
A Clinical Study of
Carglumic Acid
in Patients with Late-Onset Ornithine Transcarbamylase Deficiency
A Clinical Study of
Carglumic Acid
in Patients with Late-Onset Ornithine Transcarbamylase Deficiency ...
ornitine transcarbamylase deficiency patients
administraton of
carglumic acid
Ito Tetsuya
NULL
Complete
Not applicable
< 75age old
Both
2
Phase 4
Japan