256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details

臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2015-000512-18-Outside-EU/EEA (EUCTR)		02/03/2015	A Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for P ...	A Phase 4 Open Label, Prospective Study in Patients With Pompe Disease to Evaluate The Efficacy and ...	Pompe disease (acid alpha-glucosidase deficiency) MedDRA version: 17.1;Level: LLT;Classification cod ...	Product Name: Lumizyme ® INN or Proposed INN: ALGLUCOSIDASE ALFA Other descriptive name: rhGAA	Genzyme Corporation Inc	NULL	NA			Female: yes Male: yes	114	Phase 4	United States

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