3. 脊髄性筋萎縮症 Spinal muscular atrophy Clinical trials / Disease details

臨床試験数 : 237 / 薬物数 : 123 - (DrugBank : 29) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 75

3 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02268552 (ClinicalTrials.gov)	April 2, 2015	1/10/2014	An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)	An Open Label Multi-part First-in-human Study of Oral LMI070 in Infants With Type 1 Spinal Muscular ...	Spinal Muscular Atrophy	Drug: branaplam	Novartis Pharmaceuticals	NULL	Active, not recruiting	N/A	182 Days	All	40	Phase 1/Phase 2	Belgium;Bulgaria;Denmark;Germany;Italy;Poland;Russian Federation;Czechia;Hungary;Netherlands
2	EUCTR2014-002053-19-BE (EUCTR)	15/12/2014	04/11/2014	Clinical trial of LMI070 given by mouth to Type I SMA infant patients.	An open-label multi-part first-in-human study of oral LMI070 in infants with Type 1 spinal muscular ...	Spinal Muscular Atrophy MedDRA version: 20.1;Level: LLT;Classification code 10051203;Term: Spinal mu ...	Product Code: LMI070 INN or Proposed INN: Branaplam Other descriptive name: LMI070	Novartis Pharma Services AG	NULL	Not Recruiting			Female: yes Male: yes	44	Phase 1;Phase 2	United States;Hungary;Czech Republic;Poland;Belgium;Denmark;Bulgaria;Russian Federation;Netherlands; ...
3	EUCTR2014-002053-19-PL (EUCTR)		03/01/2018	Clinical trial of LMI070 given by mouth to Type I SMA infant patients.	An open-label multi-part first-in-human study of oral LMI070 in infants with Type 1 spinal muscular ...	Spinal Muscular Atrophy MedDRA version: 20.1;Level: LLT;Classification code 10051203;Term: Spinal mu ...	Product Code: LMI070 INN or Proposed INN: Branaplam Other descriptive name: LMI070	Novartis Pharma Services AG	NULL	Not Recruiting			Female: yes Male: yes	44	Phase 1;Phase 2	United States;Hungary;Czech Republic;Belgium;Poland;Denmark;Bulgaria;Russian Federation;Netherlands; ...

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