A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients =6 Months of Age With Infantile-onset Pompe Disease (IOPD) A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patie ...
A Prospective Observational Study to Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients =6 Months of Age With Infantile-onset Pompe Disease (IOPD) A Prospective Observational Study to Describe Clinical Outcomes of Alglucosidase Alfa Treatment in P ...
A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pedia ...
An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Efficacy of Avalglucosidase Alfa (NeoGAA, GZ402666) in Patients With Infantile-onset Pompe Disease Treated With Alglucosidase Alfa Who Demonstrate Clinical Decline or Sub-optimal Clinical Response An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Ef ...