RAAV1-CMV-GAA (study agent) Administration ( DrugBank: - )

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
256	筋型糖原病	1

256. 筋型糖原病

臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00976352 (ClinicalTrials.gov)	September 2010	13/7/2009	Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease	Phase I/II Trial of Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase ...	Pompe Disease	Drug: rAAV1-CMV-GAA (study agent) Administration;Other: RMST	University of Florida	National Heart, Lung, and Blood Institute (NHLBI)	Completed	2 Years	18 Years	All	9	Phase 1/Phase 2	United States

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