DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
Ex-vivo gene-therapy ( DrugBank: - )
1 disease
告示番号
疾患名
(ページ内リンク)
臨床試験数
65
原発性免疫不全症候群
1
65. 原発性免疫不全症候群
臨床試験数
:
500
/
薬物数
:
614
- (
DrugBank
:
119
) /
標的遺伝子数
:
92
-
標的パスウェイ数
:
217
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT01906541
(
ClinicalTrials.gov
)
July 2013
15/7/2013
Gene Therapy for X-CGD
A Phase I/II Gene Therapy Trial for X-CGD With a SIN Gammaretroviral Vector
X-linked Chronic Granulomatous Disease
Genetic:
ex-vivo gene-therapy
Hubert Serve, Prof., MD
NULL
Recruiting
18 Years
N/A
Both
5
Phase 1/Phase 2
Germany