DDrare: Database of Drug Development for Rare Diseases

Procedure: total lymphoid irradiation (DrugBank: -)

3 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
65	原発性免疫不全症候群	1
284	ダイアモンド・ブラックファン貧血	1
326	大理石骨病	1

65. 原発性免疫不全症候群　［臨床試験数：413，薬物数：581（DrugBank：97），標的遺伝子数：68，標的パスウェイ数：202］

Searched query = "Primary immunodeficiency", "X-SCID", "Reticular dysgenesis", "Adenosine deaminase deficiency", "Omenn syndrome", "Purine nucleoside phosphorylase def ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 413 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00176878 (ClinicalTrials.gov)	June 2000	12/9/2005	Stem Cell Transplant for Bone Marrow Failure Syndromes	Bone Marrow Transplantation for Non-Malignant Congenital Bone Marrow Failure Disorders	Diamond-Blackfan Anemia;Kostmann's Neutropenia;Shwachman-Diamond Syndrome	Procedure: Stem cell transplant;Drug: Fludarabine monophosphate;Procedure: Total lymphoid irradiation;Drug: Busulfan;Biological: anti-thymocyte globulin	Masonic Cancer Center, University of Minnesota	NULL	Completed	N/A	35 Years	All	10	Phase 2;Phase 3	United States

284. ダイアモンド・ブラックファン貧血　［臨床試験数：37，薬物数：110（DrugBank：34），標的遺伝子数：22，標的パスウェイ数：121］

Searched query = "Diamond-Blackfan anemia"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 37 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00176878 (ClinicalTrials.gov)	June 2000	12/9/2005	Stem Cell Transplant for Bone Marrow Failure Syndromes	Bone Marrow Transplantation for Non-Malignant Congenital Bone Marrow Failure Disorders	Diamond-Blackfan Anemia;Kostmann's Neutropenia;Shwachman-Diamond Syndrome	Procedure: Stem cell transplant;Drug: Fludarabine monophosphate;Procedure: Total lymphoid irradiation;Drug: Busulfan;Biological: anti-thymocyte globulin	Masonic Cancer Center, University of Minnesota	NULL	Completed	N/A	35 Years	All	10	Phase 2;Phase 3	United States

326. 大理石骨病　［臨床試験数：20，薬物数：52（DrugBank：14），標的遺伝子数：16，標的パスウェイ数：78］

Searched query = "Osteopetrosis"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

1 / 20 trial found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00638820 (ClinicalTrials.gov)	September 2007	11/3/2008	Reduced Intensity AlloTransplant For Osteopetrosis	Reduced Intensity Allogeneic Transplantation For Severe Osteopetrosis Incorporating A Second Cd34 Selected Graft	Osteopetrosis	Procedure: Stem Cell or Umbilical Cord Blood Transplantation;Drug: Campath, Busulfan, Clofarabine;Procedure: Total Lymphoid Irradiation	Masonic Cancer Center, University of Minnesota	NULL	Terminated	N/A	45 Years	All	3	Phase 2	United States