Retrovirus-mediated gene transfer    (DrugBank: -)

1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群2

65. 原発性免疫不全症候群 [臨床試験数:413,薬物数:581(DrugBank:97),標的遺伝子数:68,標的パスウェイ数:202
Searched query = "Primary immunodeficiency", "X-SCID", "Reticular dysgenesis", "Adenosine deaminase deficiency", "Omenn syndrome", "Purine nucleoside phosphorylase def ... show all
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.
2 / 413 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT01410825
(ClinicalTrials.gov)
July 20114/8/2011Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromePilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich SyndromeWiskott-Aldrich SyndromeBiological: Retrovirus-mediated gene transferDavid WilliamsNULLActive, not recruiting3 Months35 YearsMale5Phase 1;Phase 2United States
2NCT01129544
(ClinicalTrials.gov)
April 201021/5/2010Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral VectorMulti-institutional Phase I/II Trial Evaluating the Treatment of SCID-X1 Patients With Retrovirus-mediated Gene TransferSevere Combined ImmunodeficiencyBiological: Gene transferDavid WilliamsBoston Children's Hospital;Children's Hospital Medical Center, Cincinnati;University of California, Los AngelesActive, not recruitingN/AN/AMale8Phase 1;Phase 2United States