DDrare: Database of Drug Development for Rare Diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
65	原発性免疫不全症候群	1

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00778882 (ClinicalTrials.gov)	January 2007	21/10/2008	Gene Therapy for Chronic Granulomatous Disease in Korea	An Open-label, Uncontrolled, Single Center, Phase I/II Trial to Assess the Safety and Efficacy of Autologous Hematopoietic Stem Cells Transduced With MT-gp91 Retroviral Vector in gp91 Defective Chronic Granulomatous Disease Patients	Chronic Granulomatous Disease	Drug: VM106	Helixmith Co., Ltd.	NULL	Active, not recruiting	N/A	N/A	Male	2	Phase 1;Phase 2	Korea, Republic of

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT00778882
(ClinicalTrials.gov)

January 2007

21/10/2008

Gene Therapy for Chronic Granulomatous Disease in Korea

An Open-label, Uncontrolled, Single Center, Phase I/II Trial to Assess the Safety and Efficacy of Autologous Hematopoietic Stem Cells Transduced With MT-gp91 Retroviral Vector in gp91 Defective Chronic Granulomatous Disease Patients

Chronic Granulomatous Disease

Drug: VM106

Helixmith Co., Ltd.

NULL

Active, not recruiting

N/A

Male

Phase 1;Phase 2

Korea, Republic of