19. Lysosomal storage disease Clinical trials / Disease details
Clinical trials : 854 / Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT02124083 (ClinicalTrials.gov) | April 25, 2014 | 25/4/2014 | Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1 | Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1 | Neimann-Pick Disease | Drug: Vorinostat | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | Washington University School of Medicine;Weill Medical College of Cornell University | Completed | 18 Years | 60 Years | All | 12 | Phase 1/Phase 2 | United States |