2. Amyotrophic lateral sclerosis Clinical trials / Disease details


Clinical trials : 624 Drugs : 611 - (DrugBank : 160) / Drug target genes : 172 - Drug target pathways : 225

  
1 trial found
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1NCT04993755
(ClinicalTrials.gov)
October 1, 202119/7/2021A Phase 2a Study of TPN-101 in Patients With C9ORF72 ALS/FTDA Phase 2a Study of TPN-101 in Patients With Amyotrophic Lateral Sclerosis (ALS) and/or Frontotemporal Dementia (FTD) Associated With Hexanucleotide Repeat Expansion in the C9orf72 Gene (C9ORF72 ALS/FTD)Amyotrophic Lateral Sclerosis;Frontotemporal DementiaDrug: TPN-101, 400 mg/day;Drug: PlaceboTransposon Therapeutics, Inc.NULLRecruiting18 YearsN/AAll40Phase 2United States;France