| No. |
薬物名(臨床試験情報から抽出) |
DrugBank |
KEGG DRUG * |
KEGG GENES * |
KEGG PATHWAY |
指定難病告示番号 * |
| 1 |
Carbaglu |
Carglumic acid |
D07130 |
1件: CPS1 |
6件: Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
2件: 245, 246 |
| 2 |
Carglumic acid |
Carglumic acid |
D07130 |
1件: CPS1 |
6件: Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
2件: 245, 246 |
| 3 |
Citrate |
Citric acid |
D00037, D01222 |
- |
- |
2件: 46, 245 |
| 4 |
Disodium citrate |
Citric acid |
D00037, D01222 |
- |
- |
1件: 245 |
| 5 |
Glutamine |
L-glutamine |
D00015 |
- |
- |
6件: 87, 96, 97, 113, 245, 299 |
| 6 |
N-carbamylglutamate |
Carglumic acid |
D07130 |
1件: CPS1 |
6件: Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Biosynthesis of amino acids, Carbon metabolism, Metabolic pathways, Nitrogen metabolism |
2件: 245, 246 |
| 7 |
Ornithine |
Ornithine |
D08302 |
- |
- |
2件: 245, 251 |
| 8 |
Ornithine alpha ketoglutarate |
Ornithine |
D08302 |
- |
- |
1件: 245 |
| 9 |
Standard of care treatment |
- |
- |
- |
- |
2件: 245, 246 |