Drug Description in Trials / DrugBank / KEGG DRUG


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No. 薬物名(臨床試験情報から抽出) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY 指定難病告示番号
1(1-13C) Sodium Acetate2件: Acetate,
Sodium acetate
1件: Sodium acetate 💬 --1件: 251 💬
215N ammonium chloride (15NH4Cl)1件: Ammonium chloride1件: Ammonium chloride 💬 --1件: 251 💬
3[NA]----34件: 3, 6, 11, 13, 14, 19, 28, 35, 41, 46, 49, 50, 53, 57, 62, 63, 65, 75, 79, 85, 90, 96, 97, 98, 113, 127, 162, 195, 223, 229, 251, 294, 299, 302 💬
4[nd]----1件: 251 💬
5Acetate1件: Acetate---52件: 1, 2, 6, 10, 11, 13, 22, 35, 40, 46, 49, 51, 60, 63, 64, 65, 66, 67, 70, 71, 73, 75, 76, 77, 78, 79, 81, 83, 85, 86, 88, 89, 90, 96, 97, 113, 145, 156, 158, 162, 171, 206, 222, 223, 224, 225, 227, 235, 251, 265, 298, 299 💬
6Acetohydroxamic Acid1件: Acetohydroxamic acid1件: Acetohydroxamic acid 💬 --1件: 251 💬
7Acetohydroxamic Acid Oral Tablet [Lithostat]1件: Acetohydroxamic acid1件: Acetohydroxamic acid 💬 --1件: 251 💬
8Alanine1件: Alanine1件: Alanine 💬 --8件: 6, 13, 70, 94, 97, 251, 298, 299 💬
9ALLOGENIC HUMAN HETEROLOGOUS LIVER CELLS----1件: 251 💬
10Ammonia1件: Ammonia1件: Ammonia solution, strong 💬 --6件: 6, 17, 86, 88, 251, 296 💬
11Ammonium (15N) chloride----1件: 251 💬
12Ammonium chloride1件: Ammonium chloride1件: Ammonium chloride 💬 --3件: 96, 107, 251 💬
13ARCT-8101件: ARCT-810---1件: 251 💬
14ARCT-810Product Code: [ARCT-810]Pharmaceutical Form: Concentrate for solution for injection/infusionCurrent Sponsor code: ARCT-810Other descriptive name: mRNA codificante per Ornitina transcarbamilasi modificataConcentration unit: mg/ml milligram(s)/millilitreConcentration type: equalConcentration number: 1-Pharmaceutical form of the placebo: Solution for infusionRoute of administration of the placebo: Intravenous useProduct Name: Acetato di sodio (1,2-13C2)Product Code: [Non Applicabile]Pharmaceutical Form: Powder for oral solutionCAS Number: 56374-56-2Current Sponsor code: Acetato di sodio (1,2-13C2)Concentration unit: mg milligram(s)Concentration type: equalConcentration number: 250-1件: ARCT-810---1件: 251 💬
15Arginine1件: Arginine3件: Arginine hydrochloride ,
Arginine ,
Arginine hydrochloride 💬
--16件: 2, 21, 46, 57, 58, 67, 72, 96, 97, 98, 113, 210, 223, 225, 251, 299 💬
16Avalotcagene ontaparvovec1件: Avalotcagene ontaparvovec---1件: 251 💬
17Behavioral: Protein and calorie controlled diet----1件: 251 💬
18Carglumic Acid1件: Carglumic acid1件: Carglumic acid 💬 1件: CPS1 💬 3件: Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Nitrogen metabolism 💬3件: 245, 246, 251 💬
19Celulas hepatocitos troncales adultas alogenicas de higado expandidas----1件: 251 💬
20CMP-CPS-001----1件: 251 💬
21Diagnostic Test: Obtaining Dry Blood Spots From Healthy Children Aged 8 Days - 7 Years----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
22Diagnostic Test: Obtaining Dry Blood Spots From Healthy Children Aged 8-18 Years----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
23Diagnostic Test: Obtaining Dry Blood Spots From Healthy Newborns (Aged 1-7 Days)----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
24Diagnostic Test: Obtaining Dry Blood Spots From High-risk childrens (Aged 8 - 18 years)----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
25Diagnostic Test: Obtaining Dry Blood Spots From High-risk childrens (Aged 8 Days- 7 years)----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
26Diagnostic Test: Obtaining Dry Blood Spots From High-risk Newborns (Aged 1-7 Days)----10件: 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬
27Diagnostic Test: Urea cycle flux study1件: Urea2件: Urea ,
Urea C13 💬
--1件: 251 💬
28DTX3011件: Avalotcagene ontaparvovec---1件: 251 💬
29Genetic: AAVLK03hOTC----1件: 251 💬
30Genetic: Adenoviral Vector-Mediated Gene Transfer----1件: 251 💬
31Genetic: DTX301----1件: 251 💬
32Genetic: ECUR-506----1件: 251 💬
33Genetic: Ornithine transcarbamylase vector1件: Ornithine2件: Ornithine ,
Ornithine aspartate 💬
--1件: 251 💬
34Genetic: recombinant adenovirus containing the ornithine transcarbamylase gene1件: Ornithine2件: Ornithine ,
Ornithine aspartate 💬
--1件: 251 💬
35Genetic: scAAV8OTC----1件: 251 💬
36Glyceryl tri-(4-phenylbutyrate)----1件: 251 💬
37Glyceryl tri-(4-phenylbutyrate)(GT4P)----1件: 251 💬
38Heparesc----1件: 251 💬
39HepaStem----1件: 251 💬
40HepaStem Infusion----1件: 251 💬
41Heterologous Human Adult Liver-derived Progenitor Cells----1件: 251 💬
42Heterologous Human Adult Liver-derived Progenitor Cells (HHALPC)----1件: 251 💬
43HHALPC----1件: 251 💬
44HHLivC----1件: 251 💬
45HPN-100----1件: 251 💬
46Human Heterologous Liver Cells----1件: 251 💬
47Human heterologous liver cells (for infusion)----1件: 251 💬
48Isotopic Intravenous [13C]-Urea1件: Urea2件: Urea ,
Urea C13 💬
--1件: 251 💬
49KB195----1件: 251 💬
50MRNA encoding modified Ornithine transcarbamylase1件: Ornithine2件: Ornithine ,
Ornithine aspartate 💬
--1件: 251 💬
51MRT52011件: MRT5201---1件: 251 💬
52NaPBA----1件: 251 💬
53Neo-ASA----1件: 251 💬
54Nitric Oxide1件: Nitric Oxide1件: Nitric oxide 💬 --12件: 46, 51, 85, 86, 88, 97, 98, 210, 251, 294, 299, 340 💬
55Nitric oxide supplement1件: Nitric Oxide1件: Nitric oxide 💬 --1件: 251 💬
56Oral corticosteroids----4件: 13, 46, 97, 251 💬
57Ornithine1件: Ornithine2件: Ornithine ,
Ornithine aspartate 💬
--3件: 96, 245, 251 💬
58Other: Aminoacid, alanine-infusion1件: Alanine1件: Alanine 💬 --1件: 251 💬
59Prednisolon----11件: 46, 50, 51, 63, 66, 95, 96, 97, 222, 223, 251 💬
60PREDNISOLONE1件: Prednisolone1件: Prednisolone 💬 1件: NR3C1 💬 1件: Neuroactive ligand-receptor interaction 💬48件: 3, 11, 13, 14, 18, 25, 26, 35, 38, 39, 40, 41, 43, 44, 45, 46, 49, 50, 51, 54, 56, 57, 60, 61, 63, 64, 65, 66, 75, 81, 84, 85, 95, 96, 97, 107, 111, 113, 145, 162, 222, 223, 251, 269, 271, 296, 299, 300 💬
61Prednisone1件: Prednisone1件: Prednisone 💬 1件: NR3C1 💬 1件: Neuroactive ligand-receptor interaction 💬58件: 2, 11, 13, 14, 18, 19, 26, 28, 35, 40, 41, 42, 43, 44, 45, 46, 48, 49, 50, 51, 53, 60, 61, 63, 64, 65, 66, 79, 81, 84, 85, 86, 90, 93, 95, 96, 97, 113, 127, 145, 162, 164, 205, 222, 223, 224, 228, 251, 269, 283, 284, 285, 288, 299, 300, 303, 307, 331 💬
62Promethera HepaStem----1件: 251 💬
63Prophylactic Corticosteroid Taper Regimen----1件: 251 💬
64RAVICTI----2件: 7, 251 💬
65Reactive Corticosteroid Taper Regimen----1件: 251 💬
66Sodium acetate2件: Acetate,
Sodium acetate
1件: Sodium acetate 💬 --2件: 81, 251 💬
67Sodium acetate (1-13C)2件: Acetate,
Sodium acetate
1件: Sodium acetate 💬 --1件: 251 💬
68Sodium Ethanoate (1- 13 C)----1件: 251 💬
69Sodium Ethanoate (1-13C)----1件: 251 💬
70Sodium phenylbutyrate1件: Phenylbutyric acid1件: Sodium phenylbutyrate 💬 --5件: 2, 3, 8, 18, 251 💬
71SYNB10201件: SYNB1020---1件: 251 💬
72Urea1件: Urea2件: Urea ,
Urea C13 💬
--2件: 72, 251 💬