| 1 | 5,6,7,8-tetrahydrobiopterin | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 2 | A16ax07 | - | - | - | - | [1] 240 240 💬
|
| 3 | BH4 | - | - | - | - | [2] 51 51, 240 💬
|
| 4 | Blood samples | - | - | - | - | [12] 13 13, 41, 46, 51, 61, 96, 97, 167, 227, 240, 271, 280 💬
|
| 5 | BMN 165 | - | - | - | - | [1] 240 240 💬
|
| 6 | BMN 307 | - | - | - | - | [1] 240 240 💬
|
| 7 | BMN165 20MG/DAY | - | - | - | - | [1] 240 240 💬
|
| 8 | BMN165 40MG/DAY | - | - | - | - | [1] 240 240 💬
|
| 9 | CBT102-A capsule | - | - | - | - | [1] 240 240 💬
|
| 10 | CDX 6114 | - | - | - | - | [1] 240 240 💬
|
| 11 | CNSA-001 | - | - | - | - | [1] 240 240 💬
|
| 12 | Cohort 1 0.225G | - | - | - | - | [1] 240 240 💬
|
| 13 | Cohort 2 0.75G | - | - | - | - | [1] 240 240 💬
|
| 14 | Cohort 3 2.25 G | - | - | - | - | [1] 240 240 💬
|
| 15 | Corn/SOY OIL | [1] Corn Corn | - | - | - | [1] 240 240 💬
|
| 16 | Diet treatment | - | - | - | - | [1] 240 240 💬
|
| 17 | Dietary supplement FOR PKU patients | - | - | - | - | [1] 240 240 💬
|
| 18 | Docosahexaenoic acid | [1] Doconexent Doconexent | - | - | - | [6] 6 6, 49, 90, 94, 240, 299 💬
|
| 19 | Free amino acids intake | - | - | - | - | [1] 240 240 💬
|
| 20 | Glycomacropeptide-based protein substitute | - | - | - | - | [1] 240 240 💬
|
| 21 | Glytactin | - | - | - | - | [1] 240 240 💬
|
| 22 | GMP intervention product | - | - | - | - | [1] 240 240 💬
|
| 23 | Hepatocyte transplant | - | - | - | - | [1] 240 240 💬
|
| 24 | HMI-102 | - | - | - | - | [1] 240 240 💬
|
| 25 | HMI-103 | [1] HMI-103 HMI-103 | - | - | - | [1] 240 240 💬
|
| 26 | Immunosuppression | - | - | - | - | [1] 240 240 💬
|
| 27 | Iron supplementation | - | - | - | - | [1] 240 240 💬
|
| 28 | JNT-517 suspension | [1] JNT-517 JNT-517 | - | - | - | [1] 240 240 💬
|
| 29 | JNT-517 tablet | [1] JNT-517 JNT-517 | - | - | - | [1] 240 240 💬
|
| 30 | Kuvan | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 31 | Kuvan 100MG soluble tablet | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 32 | Kuvantm therapy | - | - | - | - | [1] 240 240 💬
|
| 33 | L-AA | - | - | - | - | [1] 240 240 💬
|
| 34 | L-carnitine | [1] Levocarnitine Levocarnitine | [2] Levocarnitine chloride
Levocarnitine chloride
,
Levocarnitine
💬
| - | - | [5] 13 13, 46, 86, 96, 240 💬
|
| 35 | Large neutral amino acid therapy | - | - | - | - | [1] 240 240 💬
|
| 36 | Liver biopsy | - | - | - | - | [3] 171 171, 231, 240 💬
|
| 37 | Liver evaluation | - | - | - | - | [1] 240 240 💬
|
| 38 | LOW calorie protein substitute | - | - | - | - | [1] 240 240 💬
|
| 39 | Meal challenge | - | - | - | - | [1] 240 240 💬
|
| 40 | Medikinet | - | - | - | - | [1] 240 240 💬
|
| 41 | Moxifloxacin | [1] Moxifloxacin Moxifloxacin | [3] Moxifloxacin hydrochloride
Moxifloxacin hydrochloride
,
Moxifloxacin
,
Moxifloxacin hydrochloride monohydrate
💬
| - | - | [7] 2 2, 6, 46, 49, 85, 240, 299 💬
|
| 42 | MRNA-3210 | - | - | - | - | [1] 240 240 💬
|
| 43 | NAP | - | - | - | - | [2] 96 96, 240 💬
|
| 44 | Neuro-psychological assessment | - | - | - | - | [1] 240 240 💬
|
| 45 | NGGT002 | - | - | - | - | [1] 240 240 💬
|
| 46 | Normal (control) diet | - | - | - | - | [1] 240 240 💬
|
| 47 | Palynziq | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 48 | Pegvaliase | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 49 | Pegvaliase-pqpz | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 50 | Phenoptin | - | - | - | - | [2] 124 124, 240 💬
|
| 51 | Phenylalanine | [1] Phenylalanine Phenylalanine | [1] Phenylalanine
Phenylalanine
💬
| - | - | [1] 240 240 💬
|
| 52 | Phenylalanine (PHE)-restricted diet | [1] Phenylalanine Phenylalanine | [1] Phenylalanine
Phenylalanine
💬
| - | - | [1] 240 240 💬
|
| 53 | Phenylalanine restricted diet | [1] Phenylalanine Phenylalanine | [1] Phenylalanine
Phenylalanine
💬
| - | - | [1] 240 240 💬
|
| 54 | Phenylalanine-free milk | [1] Phenylalanine Phenylalanine | [1] Phenylalanine
Phenylalanine
💬
| - | - | [1] 240 240 💬
|
| 55 | Phenylalanine-free protein substitute tablets | [1] Phenylalanine Phenylalanine | [1] Phenylalanine
Phenylalanine
💬
| - | - | [1] 240 240 💬
|
| 56 | Phenylketonuria-type diet | - | - | - | - | [1] 240 240 💬
|
| 57 | PKU easy microtabs plus | - | - | - | - | [1] 240 240 💬
|
| 58 | PKU explore | - | - | - | - | [1] 240 240 💬
|
| 59 | PKU golike | - | - | - | - | [1] 240 240 💬
|
| 60 | PKU sphere | - | - | - | - | [1] 240 240 💬
|
| 61 | PKU sphere liquid | - | - | - | - | [1] 240 240 💬
|
| 62 | PKU start | - | - | - | - | [1] 240 240 💬
|
| 63 | PKU UP | - | - | - | - | [1] 240 240 💬
|
| 64 | PKU/TYR GMP protein substitute | - | - | - | - | [1] 240 240 💬
|
| 65 | Preparative radiation therapy | - | - | - | - | [1] 240 240 💬
|
| 66 | Protein intake | - | - | - | - | [1] 240 240 💬
|
| 67 | PTC923 | - | - | - | - | [1] 240 240 💬
|
| 68 | Ravpal-PEG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 69 | Ravpal-PEG 0.001 MG/KG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 70 | Ravpal-PEG 0.003 MG/KG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 71 | Ravpal-PEG 0.01 MG/KG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 72 | Ravpal-PEG 0.03 MG/KG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 73 | Ravpal-PEG 0.1 MG/KG | [1] Pegvaliase Pegvaliase | [1] Pegvaliase
Pegvaliase
💬
| [1] phhA phhA 💬
| [3] Folate biosynthesis Folate biosynthesis, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1] 240 240 💬
|
| 74 | RDD TO palynziq | - | - | - | - | [1] 240 240 💬
|
| 75 | Restricted phenylalanine diet | - | - | - | - | [1] 240 240 💬
|
| 76 | Routine | - | - | - | - | [1] 240 240 💬
|
| 77 | RTX-134 | - | - | - | - | [1] 240 240 💬
|
| 78 | Sapropterin | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [3] 86 86, 124, 240 💬
|
| 79 | Sapropterin dihydrochloride | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 80 | Sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 81 | Sapropterin dihydrocholoride | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 82 | Sapropterin hydrochloride | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 83 | Sapropterin, sapropterin dihydrochloride | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 84 | Sapropterin, sapropterin hydrochloride | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 85 | Sapropterindihydrochloride | - | - | - | - | [1] 240 240 💬
|
| 86 | Saproterin dihydrochloride | - | - | - | - | [1] 240 240 💬
|
| 87 | SAR444836 | - | - | - | - | [1] 240 240 💬
|
| 88 | Sepiapterin | [1] Sepiapterin Sepiapterin | [1] Sepiapterin
Sepiapterin
💬
| - | - | [1] 240 240 💬
|
| 89 | SYNB1618 | - | - | - | - | [1] 240 240 💬
|
| 90 | SYNB1934 | [1] Labafenogene marselecobac Labafenogene marselecobac | - | - | - | [1] 240 240 💬
|
| 91 | SYNB1934v1 | - | - | - | - | [1] 240 240 💬
|
| 92 | Synergy | - | - | - | - | [1] 240 240 💬
|
| 93 | T1401 | - | - | - | - | [1] 240 240 💬
|
| 94 | Tetrahydrobiopterin | [1] Sapropterin Sapropterin | [2] Sapropterin dihydrochloride
Sapropterin dihydrochloride
,
Sapropterin
💬
| - | - | [1] 240 240 💬
|
| 95 | Whole body PHE oxidation testing | - | - | - | - | [1] 240 240 💬
|