| 1 | AAVrh10-PCCA high dose | - | - | - | - | [1] 245 245 💬
|
| 2 | AAVrh10-PCCA low dose | - | - | - | - | [1] 245 245 💬
|
| 3 | AAVrh10-PCCA middle dose | - | - | - | - | [1] 245 245 💬
|
| 4 | BBP-671 | [1] BBP-671 BBP-671 | - | - | - | [2] 245 245, 246 💬
|
| 5 | Carbaglu | - | - | - | - | [2] 245 245, 246 💬
|
| 6 | Carglumic Acid | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬
| [1] CPS1 CPS1 💬
| [3] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Nitrogen metabolism 💬 | [3] 245 245, 246, 251 💬
|
| 7 | Carglumic Acid (Carbaglu®) | [1] Carglumic acid Carglumic acid | [1] Carglumic acid
Carglumic acid
💬
| [1] CPS1 CPS1 💬
| [3] Alanine, aspartate and glutamate metabolism Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Nitrogen metabolism 💬 | [2] 245 245, 246 💬
|
| 8 | CX-016492 | - | - | - | - | [1] 245 245 💬
|
| 9 | CX-017950 | - | - | - | - | [1] 245 245 💬
|
| 10 | Dimebutic acid | - | - | - | - | [2] 245 245, 246 💬
|
| 11 | Disodium citrate | - | - | - | - | [1] 245 245 💬
|
| 12 | Glutamine | [1] L-Glutamine L-Glutamine | [1] Glutamine
Glutamine
💬
| - | - | [7] 87 87, 89, 96, 97, 113, 245, 299 💬
|
| 13 | HST5040 | - | - | - | - | [2] 245 245, 246 💬
|
| 14 | MRNA-3927 | [1] mRNA-3927 mRNA-3927 | - | - | - | [1] 245 245 💬
|
| 15 | N-carbamylglutamate | - | - | - | - | [2] 245 245, 246 💬
|
| 16 | Ornithine | [1] Ornithine Ornithine | [2] Ornithine
Ornithine
,
Ornithine aspartate
💬
| - | - | [3] 96 96, 245, 251 💬
|
| 17 | Ornithine alpha ketoglutarate | [1] Ornithine Ornithine | [2] Ornithine
Ornithine
,
Ornithine aspartate
💬
| - | - | [1] 245 245 💬
|
| 18 | Other: Standard of Care | - | - | - | - | [11] 13 13, 49, 57, 64, 79, 85, 95, 96, 97, 245, 246 💬
|
| 19 | Standard of Care Treatment | - | - | - | - | [6] 11 11, 49, 53, 96, 245, 246 💬
|