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KEGG DRUG

Search results

No.

Drug (Description in trials)

DrugBank

KEGG DRUG

KEGG GENES

KEGG PATHWAY

Disease ID

(1-13C) Sodium Acetate

[2] Acetate,
Sodium acetate

[1] Sodium acetate 💬

[1] 251 💬

15N ammonium chloride (15NH4Cl)

[1] Ammonium chloride

[1] Ammonium chloride 💬

[1] 251 💬

[NA]

[34] 3, 6, 11, 13, 14, 19, 28, 35, 41, 46, 49, 50, 53, 57, 62, 63, 65, 75, 79, 85, 90, 96, 97, 98, 113, 127, 162, 195, 223, 229, 251, 294, 299, 302 💬

Disease ID	Name
3	Spinal muscular atrophy
6	Parkinson disease
11	Myasthenia gravis
13	Multiple sclerosis/Neuromyelitis optica
14	Chronic inflammatory demyelinating polyneuropathy
19	Lysosomal storage disease
28	Systemic amyloidosis
35	Pemphigus
41	Giant cell arteritis
46	Malignant rheumatoid arthritis
49	Systemic lupus erythematosus
50	Dermatomyositis
53	Sjogren syndrome
57	Idiopathic dilated cardiomyopathy
62	Paroxysmal nocturnal hemoglobinuria
63	Idiopathic thrombocytopenic purpura
65	Primary immunodeficiency
75	Cushing disease
79	Homozygous familial hypercholesterolemia
85	Idiopathic interstitial pneumonia
90	Retinitis pigmentosa
96	Crohn disease
97	Ulcerative colitis
98	Eosinophilic gastro-intestinal disorder
113	Muscular dystrophy
127	Frontotemporal lobar degeneration
162	Pemphigoid
195	Noonan syndrome
223	Primary membranoproliferative glomerulonephritis
229	Autoimmune pulmonary alveolar proteinosis
251	Urea cycle disorder
294	Congenital diaphragmatic hernia
299	Cystic fibrosis
302	Leber hereditary optic neuropathy

[nd]

[1] 251 💬

Acetate

[1] Acetate

[52] 1, 2, 6, 10, 11, 13, 22, 35, 40, 46, 49, 51, 60, 63, 64, 65, 66, 67, 70, 71, 73, 75, 76, 77, 78, 79, 81, 83, 85, 86, 88, 89, 90, 96, 97, 113, 145, 156, 158, 162, 171, 206, 222, 223, 224, 225, 227, 235, 251, 265, 298, 299 💬

Disease ID	Name
1	Spinal and bulbar muscular atrophy
2	Amyotrophic lateral sclerosis
6	Parkinson disease
10	Charcot-Marie-Tooth disease
11	Myasthenia gravis
13	Multiple sclerosis/Neuromyelitis optica
22	Moyamoya disease
35	Pemphigus
40	Takayasu arteritis
46	Malignant rheumatoid arthritis
49	Systemic lupus erythematosus
51	Scleroderma
60	Aplastic anemia
63	Idiopathic thrombocytopenic purpura
64	Thrombotic thrombocytopenic purpura
65	Primary immunodeficiency
66	IgA nephropathy
67	Polycystic kidney disease
70	Spinal stenosis
71	Idiopathic osteonecrosis of the femoral head
73	TSH-secreting pituitary adenoma
75	Cushing disease
76	Pituitary gonadotropin secretion hyperthyroidism
77	Growth hormone secreting pituitary adenoma
78	Hypopituitarism
79	Homozygous familial hypercholesterolemia
81	Congenital adrenal hyperplasia
83	Addison disease
85	Idiopathic interstitial pneumonia
86	Pulmonary arterial hypertension
88	Chronic thromboembolic pulmonary hypertension
89	Lymphangioleiomyomatosis
90	Retinitis pigmentosa
96	Crohn disease
97	Ulcerative colitis
113	Muscular dystrophy
145	West syndrome
156	Rett syndrome
158	Tuberous sclerosis
162	Pemphigoid
171	Wilson disease
206	Fragile X syndrome
222	Primary nephrotic syndrome
223	Primary membranoproliferative glomerulonephritis
224	Purpura nephritis
225	Congenital nephrogenic diabetes insipidus
227	Osler disease
235	Hypoparathyroidism
251	Urea cycle disorder
265	Lipodystrophy
298	Hereditary pancreatitis
299	Cystic fibrosis

Acetohydroxamic Acid

[1] Acetohydroxamic acid

[1] Acetohydroxamic acid 💬

[1] 251 💬

Acetohydroxamic Acid Oral Tablet [Lithostat]

[1] Acetohydroxamic acid

[1] Acetohydroxamic acid 💬

[1] 251 💬

Alanine

[1] Alanine

[1] Alanine 💬

[8] 6, 13, 70, 94, 97, 251, 298, 299 💬

Disease ID	Name
6	Parkinson disease
13	Multiple sclerosis/Neuromyelitis optica
70	Spinal stenosis
94	Primary sclerosing cholangitis
97	Ulcerative colitis
251	Urea cycle disorder
298	Hereditary pancreatitis
299	Cystic fibrosis

ALLOGENIC HUMAN HETEROLOGOUS LIVER CELLS

[1] 251 💬

Ammonia

[1] Ammonia

[1] Ammonia solution, strong 💬

[6] 6, 17, 86, 88, 251, 296 💬

Ammonium (15N) chloride

[1] 251 💬

Ammonium chloride

[1] Ammonium chloride

[1] Ammonium chloride 💬

[3] 96, 107, 251 💬

ARCT-810

[1] ARCT-810

[1] 251 💬

ARCT-810Product Code: [ARCT-810]Pharmaceutical Form: Concentrate for solution for injection/infusionCurrent Sponsor code: ARCT-810Other descriptive name: mRNA codificante per Ornitina transcarbamilasi modificataConcentration unit: mg/ml milligram(s)/millilitreConcentration type: equalConcentration number: 1-Pharmaceutical form of the placebo: Solution for infusionRoute of administration of the placebo: Intravenous useProduct Name: Acetato di sodio (1,2-13C2)Product Code: [Non Applicabile]Pharmaceutical Form: Powder for oral solutionCAS Number: 56374-56-2Current Sponsor code: Acetato di sodio (1,2-13C2)Concentration unit: mg milligram(s)Concentration type: equalConcentration number: 250-

[1] ARCT-810

[1] 251 💬

Arginine

[1] Arginine

[3] Arginine hydrochloride ,
Arginine ,
Arginine hydrochloride 💬

[16] 2, 21, 46, 57, 58, 67, 72, 96, 97, 98, 113, 210, 223, 225, 251, 299 💬

Disease ID	Name
2	Amyotrophic lateral sclerosis
21	Mitochondrial disease
46	Malignant rheumatoid arthritis
57	Idiopathic dilated cardiomyopathy
58	Hypertrophic cardiomyopathy
67	Polycystic kidney disease
72	Pituitary ADH secretion disorder
96	Crohn disease
97	Ulcerative colitis
98	Eosinophilic gastro-intestinal disorder
113	Muscular dystrophy
210	Single Ventricle
223	Primary membranoproliferative glomerulonephritis
225	Congenital nephrogenic diabetes insipidus
251	Urea cycle disorder
299	Cystic fibrosis

Avalotcagene ontaparvovec

[1] Avalotcagene ontaparvovec

[1] 251 💬

Behavioral: Protein and calorie controlled diet

[1] 251 💬

Carglumic Acid

[1] Carglumic acid

[1] Carglumic acid 💬

[1] CPS1 💬

[3] Alanine, aspartate and glutamate metabolism, Arginine biosynthesis, Nitrogen metabolism 💬

[3] 245, 246, 251 💬

Celulas hepatocitos troncales adultas alogenicas de higado expandidas

[1] 251 💬

CMP-CPS-001

[1] 251 💬

Diagnostic Test: Obtaining Dry Blood Spots From Healthy Children Aged 8 Days - 7 Years

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Obtaining Dry Blood Spots From Healthy Children Aged 8-18 Years

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Obtaining Dry Blood Spots From Healthy Newborns (Aged 1-7 Days)

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Obtaining Dry Blood Spots From High-risk childrens (Aged 8 - 18 years)

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Obtaining Dry Blood Spots From High-risk childrens (Aged 8 Days- 7 years)

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Obtaining Dry Blood Spots From High-risk Newborns (Aged 1-7 Days)

[10] 244, 247, 251, 255, 316, 321, 322, 324, 337, 344 💬

Disease ID	Name
244	Maple syrup urine disease
247	Isovaleric acidemia
251	Urea cycle disorder
255	Multiple carboxylase deficiency
316	Carnitine cycle disorder
321	Non-ketotic hyperglycinemia
322	Beta-ketothiolase deficiency
324	Methylglutaconic aciduria
337	Homocystinuria
344	Very long-chain acyl-CoA dehydrogenase deficiency

Diagnostic Test: Urea cycle flux study

[1] Urea

[2] Urea ,
Urea C13 💬

[1] 251 💬

DTX301

[1] Avalotcagene ontaparvovec

[1] 251 💬

Genetic: AAVLK03hOTC

[1] 251 💬

Genetic: Adenoviral Vector-Mediated Gene Transfer

[1] 251 💬

Genetic: DTX301

[1] 251 💬

Genetic: ECUR-506

[1] 251 💬

Genetic: Ornithine transcarbamylase vector

[1] Ornithine

[2] Ornithine ,
Ornithine aspartate 💬

[1] 251 💬

Genetic: recombinant adenovirus containing the ornithine transcarbamylase gene

[1] Ornithine

[2] Ornithine ,
Ornithine aspartate 💬

[1] 251 💬

Genetic: scAAV8OTC

[1] 251 💬

Glyceryl tri-(4-phenylbutyrate)

[1] 251 💬

Glyceryl tri-(4-phenylbutyrate)(GT4P)

[1] 251 💬

Heparesc

[1] 251 💬

HepaStem

[1] 251 💬

HepaStem Infusion

[1] 251 💬

Heterologous Human Adult Liver-derived Progenitor Cells

[1] 251 💬

Heterologous Human Adult Liver-derived Progenitor Cells (HHALPC)

[1] 251 💬

HHALPC

[1] 251 💬

HHLivC

[1] 251 💬

HPN-100

[1] 251 💬

Human Heterologous Liver Cells

[1] 251 💬

Human heterologous liver cells (for infusion)

[1] 251 💬

Isotopic Intravenous [13C]-Urea

[1] Urea

[2] Urea ,
Urea C13 💬

[1] 251 💬

KB195

[1] 251 💬

MRNA encoding modified Ornithine transcarbamylase

[1] Ornithine

[2] Ornithine ,
Ornithine aspartate 💬

[1] 251 💬

MRT5201

[1] MRT5201

[1] 251 💬

NaPBA

[1] 251 💬

Neo-ASA

[1] 251 💬

Nitric Oxide

[1] Nitric Oxide

[1] Nitric oxide 💬

[12] 46, 51, 85, 86, 88, 97, 98, 210, 251, 294, 299, 340 💬

Disease ID	Name
46	Malignant rheumatoid arthritis
51	Scleroderma
85	Idiopathic interstitial pneumonia
86	Pulmonary arterial hypertension
88	Chronic thromboembolic pulmonary hypertension
97	Ulcerative colitis
98	Eosinophilic gastro-intestinal disorder
210	Single Ventricle
251	Urea cycle disorder
294	Congenital diaphragmatic hernia
299	Cystic fibrosis
340	Primary ciliary dyskinesia

Nitric oxide supplement

[1] Nitric Oxide

[1] Nitric oxide 💬

[1] 251 💬

Oral corticosteroids

[4] 13, 46, 97, 251 💬

Ornithine

[1] Ornithine

[2] Ornithine ,
Ornithine aspartate 💬

[3] 96, 245, 251 💬

Other: Aminoacid, alanine-infusion

[1] Alanine

[1] Alanine 💬

[1] 251 💬

Prednisolon

[11] 46, 50, 51, 63, 66, 95, 96, 97, 222, 223, 251 💬

Disease ID	Name
46	Malignant rheumatoid arthritis
50	Dermatomyositis
51	Scleroderma
63	Idiopathic thrombocytopenic purpura
66	IgA nephropathy
95	Autoimmune hepatitis
96	Crohn disease
97	Ulcerative colitis
222	Primary nephrotic syndrome
223	Primary membranoproliferative glomerulonephritis
251	Urea cycle disorder

PREDNISOLONE

[1] Prednisolone

[1] Prednisolone 💬

[1] NR3C1 💬

[1] Neuroactive ligand-receptor interaction 💬

[48] 3, 11, 13, 14, 18, 25, 26, 35, 38, 39, 40, 41, 43, 44, 45, 46, 49, 50, 51, 54, 56, 57, 60, 61, 63, 64, 65, 66, 75, 81, 84, 85, 95, 96, 97, 107, 111, 113, 145, 162, 222, 223, 251, 269, 271, 296, 299, 300 💬

Disease ID	Name
3	Spinal muscular atrophy
11	Myasthenia gravis
13	Multiple sclerosis/Neuromyelitis optica
14	Chronic inflammatory demyelinating polyneuropathy
18	Spinocerebellar degeneration
25	Progressive multifocal leukoencephalopathy
26	HTLV-1-associated myelopathy
35	Pemphigus
38	Stevens-Johnson syndrome
39	Toxic epidermal necrolysis
40	Takayasu arteritis
41	Giant cell arteritis
43	Microscopic polyangiitis
44	Wegener granulomatosis
45	Eosinophilic granulomatosis with Polyangiitis
46	Malignant rheumatoid arthritis
49	Systemic lupus erythematosus
50	Dermatomyositis
51	Scleroderma
54	Adult still disease
56	Behcet disease
57	Idiopathic dilated cardiomyopathy
60	Aplastic anemia
61	Autoimmune hemolytic anemia
63	Idiopathic thrombocytopenic purpura
64	Thrombotic thrombocytopenic purpura
65	Primary immunodeficiency
66	IgA nephropathy
75	Cushing disease
81	Congenital adrenal hyperplasia
84	Sarcoidosis
85	Idiopathic interstitial pneumonia
95	Autoimmune hepatitis
96	Crohn disease
97	Ulcerative colitis
107	Juvenile idiopathic arthritis
111	Congenital myopathy
113	Muscular dystrophy
145	West syndrome
162	Pemphigoid
222	Primary nephrotic syndrome
223	Primary membranoproliferative glomerulonephritis
251	Urea cycle disorder
269	Pyogenic arthritis
271	Ankylosing spondylitis
296	Biliary atresia
299	Cystic fibrosis
300	IgG4-related disease

Prednisone

[1] Prednisone

[1] Prednisone 💬

[1] NR3C1 💬

[1] Neuroactive ligand-receptor interaction 💬

[58] 2, 11, 13, 14, 18, 19, 26, 28, 35, 40, 41, 42, 43, 44, 45, 46, 48, 49, 50, 51, 53, 60, 61, 63, 64, 65, 66, 79, 81, 84, 85, 86, 90, 93, 95, 96, 97, 113, 127, 145, 162, 164, 205, 222, 223, 224, 228, 251, 269, 283, 284, 285, 288, 299, 300, 303, 307, 331 💬

Disease ID	Name
2	Amyotrophic lateral sclerosis
11	Myasthenia gravis
13	Multiple sclerosis/Neuromyelitis optica
14	Chronic inflammatory demyelinating polyneuropathy
18	Spinocerebellar degeneration
19	Lysosomal storage disease
26	HTLV-1-associated myelopathy
28	Systemic amyloidosis
35	Pemphigus
40	Takayasu arteritis
41	Giant cell arteritis
42	Polyarteritis nodosa
43	Microscopic polyangiitis
44	Wegener granulomatosis
45	Eosinophilic granulomatosis with Polyangiitis
46	Malignant rheumatoid arthritis
48	Primary antiphospholipid syndrome
49	Systemic lupus erythematosus
50	Dermatomyositis
51	Scleroderma
53	Sjogren syndrome
60	Aplastic anemia
61	Autoimmune hemolytic anemia
63	Idiopathic thrombocytopenic purpura
64	Thrombotic thrombocytopenic purpura
65	Primary immunodeficiency
66	IgA nephropathy
79	Homozygous familial hypercholesterolemia
81	Congenital adrenal hyperplasia
84	Sarcoidosis
85	Idiopathic interstitial pneumonia
86	Pulmonary arterial hypertension
90	Retinitis pigmentosa
93	Primary biliary cholangitis
95	Autoimmune hepatitis
96	Crohn disease
97	Ulcerative colitis
113	Muscular dystrophy
127	Frontotemporal lobar degeneration
145	West syndrome
162	Pemphigoid
164	Oculocutaneous albinism
205	Fragile X syndrome related disease
222	Primary nephrotic syndrome
223	Primary membranoproliferative glomerulonephritis
224	Purpura nephritis
228	Bronchiolitis obliterans
251	Urea cycle disorder
269	Pyogenic arthritis
283	Acquired pure red cell aplasia
284	Diamond-Blackfan anemia
285	Fanconi anemia
288	Autoimmune acquired coagulation factor deficiency
299	Cystic fibrosis
300	IgG4-related disease
303	Usher syndrome
307	Canavan disease
331	Idiopathic multicentric castleman disease