| 1 | Blinded CDCA 250 mg TID | - | - | - | - | [1] 263 263 💬
|
| 2 | Blood sampling for Cholestanol Analysis | - | - | - | - | [1] 263 263 💬
|
| 3 | Blood tests | - | - | - | - | [3] 46 46, 226, 263 💬
|
| 4 | CDCA Weight-Based Dose TID | - | - | - | - | [1] 263 263 💬
|
| 5 | Chenodeoxycholic acid | [1] Chenodeoxycholic acid Chenodeoxycholic acid | [1] Chenodiol
Chenodiol
💬
| [1] NR1H4 NR1H4 💬
| [1] Bile secretion Bile secretion 💬 | [5] 20 20, 86, 96, 234, 263 💬
|
| 6 | Chenodeoxycholic acid leadiant | [1] Chenodeoxycholic acid Chenodeoxycholic acid | [1] Chenodiol
Chenodiol
💬
| [1] NR1H4 NR1H4 💬
| [1] Bile secretion Bile secretion 💬 | [1] 263 263 💬
|
| 7 | Genetic: Mutation Analysis | - | - | - | - | [1] 263 263 💬
|
| 8 | Lovastatin | [1] Lovastatin Lovastatin | [1] Lovastatin
Lovastatin
💬
| [1] HMGCR HMGCR 💬
| [3] AMPK signaling pathway AMPK signaling pathway, Bile secretion, Terpenoid backbone biosynthesis 💬 | [11] 6 6, 34, 46, 79, 156, 160, 195, 206, 263, 280, 310 💬
|
| 9 | Open-Label CDCA 250 mg TID | - | - | - | - | [1] 263 263 💬
|
| 10 | Other: Blood sampling for cholestanol analysis | - | - | - | - | [1] 263 263 💬
|
| 11 | Rescue Medication CDCA 250 mg TID | - | - | - | - | [1] 263 263 💬
|