120. 遺伝性ジストニア Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 5 / 薬物数 : 6 - (DrugBank : 3) / 標的遺伝子数 : 17 - 標的パスウェイ数 : 26
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Ampicillin
University of Florida
2011 Phase 1 NCT01433757 United States
Chlorpromazine
Department of Neurology, Osaka Neurological Institute
2017 - JPRN-UMIN000027430 Japan
Kumamoto Neurosurgical Hospital
2024 - JPRN-UMIN000056138 Japan
Levodopa
Department of Neurology, Osaka Neurological Institute
2017 - JPRN-UMIN000027430 Japan
Kumamoto Neurosurgical Hospital
2024 - JPRN-UMIN000056138 Japan
Mingo
Sunshine Care Foundation
2017 - NCT03019458 Philippines
Sugar pill
University of Florida
2011 Phase 1 NCT01433757 United States
Whole exome sequencing
Institute of Child Health
2018 - NCT03857607 United Kingdom
University of Florida
2011 Phase 1 NCT01433757 United States
Chlorpromazine
Department of Neurology, Osaka Neurological Institute
2017 - JPRN-UMIN000027430 Japan
Kumamoto Neurosurgical Hospital
2024 - JPRN-UMIN000056138 Japan
Levodopa
Department of Neurology, Osaka Neurological Institute
2017 - JPRN-UMIN000027430 Japan
Kumamoto Neurosurgical Hospital
2024 - JPRN-UMIN000056138 Japan
Mingo
Sunshine Care Foundation
2017 - NCT03019458 Philippines
Sugar pill
University of Florida
2011 Phase 1 NCT01433757 United States
Whole exome sequencing
Institute of Child Health
2018 - NCT03857607 United Kingdom
