125. 神経軸索スフェロイド形成を伴う遺伝性びまん性白質脳症 Disease details / Clinical trials / Drug dev / DR info /
臨床試験数 : 1 / 薬物数 : 4 - (DrugBank : 1) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
IMD preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis haploidentical only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis haploidentical only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Osteopetrosis only preparative regimen
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2014 Phase 2 NCT02171104 United States