140. ドラベ症候群 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 139 / 薬物数 : 49 - (DrugBank : 17) / 標的遺伝子数 : 53 - 標的パスウェイ数 : 67

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
12-lead ECG
   Gillette Children's Specialty Healthcare
      2017   Phase 1/Phase 2   NCT02815540   United States
Ataluren
   NYU Langone Health
      2016   Phase 2   NCT02758626   United States
BMB-101
   Bright Minds Biosciences Pty Ltd
      2024   Phase 2   NCT06401538   Australia
Cannabidiol
   GW Research Ltd
      2015   Phase 3   EUCTR2014-002939-34-NL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-002939-34-ES   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-PL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-NL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-GB   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-FR   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-ES   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   -   EUCTR2014-000995-24-PL   France;Poland;United Kingdom;United States
      2014   Phase 3   EUCTR2014-002939-34-GB   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2014   Phase 2;Phase 3   EUCTR2014-000995-24-GB   France;Poland;United Kingdom;United States
      -   Phase 3   EUCTR2014-002939-34-PL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
   Gillette Children's Specialty Healthcare
      2017   Phase 1/Phase 2   NCT02815540   United States
   Jazz Pharmaceuticals
      2021   Phase 4   NCT05044819   United States
   Yonsei University
      2020   Phase 3   NCT04611438   Korea, Republic of
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2018   Phase 1   NCT03467113   United States
Cannabidiol oral solution
   INSYS Therapeutics Inc
      2017   Phase 3   NCT02318563   -
Carbidopa
   Natsume Jun
      2020   Phase 4   JPRN-jRCTs041190116   -
CBD
   GW Research Ltd
      2015   Phase 3   EUCTR2014-002939-34-NL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-002939-34-ES   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-PL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-NL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-GB   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-FR   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-ES   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   -   EUCTR2014-000995-24-PL   France;Poland;United Kingdom;United States
      2014   Phase 3   EUCTR2014-002939-34-GB   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2014   Phase 2;Phase 3   EUCTR2014-000995-24-GB   France;Poland;United Kingdom;United States
      -   Phase 3   EUCTR2014-002939-34-PL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
CBD: GT4 transdermal delivery system
   Alexander Rotenberg
      2025   Phase 1/Phase 2   NCT06738732   United States
Clemizole HCL
   Epygenix
      2020   Phase 3   NCT04462770   Canada;Georgia;Hungary;Poland;Romania;Spain;United Kingdom;United States
Clemizole hydrochloride
   Epygenix
      2019   Phase 1   NCT04069689   United States
   Epygenix Therapeutics, Inc.
      2023   Phase 2   EUCTR2021-003425-30-HU   Bulgaria;Canada;Georgia;Hungary;India;Poland;Romania;Spain;United Kingdom;United States
      2022   Phase 2   EUCTR2021-003425-30-ES   Canada;Hungary;Poland;Spain;United Kingdom;United States
      -   Phase 2   EUCTR2021-003425-30-PL   Bulgaria;Canada;Georgia;Hungary;India;Poland;Romania;Spain;United Kingdom;United States
Clobazam
   H. Lundbeck A/S
      2015   Phase 3   NCT02187809   Mexico;United States
      2015   Phase 3   NCT02174094   Mexico;United States
   ISTITUTO C. MONDINO
      2007   -   EUCTR2007-003702-95-IT   Italy
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
   West China Second University Hospital, Sichuan University
      2024   Phase 4   ChiCTR2400088523   China
Diacomit
   BIOCODEX
      2007   Phase 2   EUCTR2007-001784-30-FR   France
   Meiji Seika Pharma Co., Ltd.
      2012   -   JPRN-jRCT1080225085   Japan
Epidiolex 100 MG/ML oral solution
   Elizabeth Donner
      2025   Phase 4   NCT06924827   Canada
   Jazz Pharmaceuticals
      2025   -   NCT05485831   Italy
EPX-100
   Epygenix
      2019   Phase 1   NCT04069689   United States
   Epygenix Therapeutics, Inc.
      2023   Phase 2   EUCTR2021-003425-30-HU   Bulgaria;Canada;Georgia;Hungary;India;Poland;Romania;Spain;United Kingdom;United States
      2022   Phase 2   EUCTR2021-003425-30-ES   Canada;Hungary;Poland;Spain;United Kingdom;United States
      -   Phase 2   EUCTR2021-003425-30-PL   Bulgaria;Canada;Georgia;Hungary;India;Poland;Romania;Spain;United Kingdom;United States
ETX101
   Encoded Therapeutics
      2024   Phase 1/Phase 2   NCT06283212   United Kingdom
      2024   Phase 1/Phase 2   NCT06112275   Australia
      2024   Phase 1/Phase 2   NCT05419492   United States
Exome and/or whole genome sequencing
   Boston Children's Hospital
      2010   -   NCT01858285   United States
Fenfluramina cloridrato
   ZOGENIX INTERNATIONAL LTD
      2016   Phase 3   EUCTR2015-004167-37-IT   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
   Zogenix International Limited
      2019   Phase 3   EUCTR2019-001331-31-IT   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
Fenfluramine
   UCB BIOSCIENCES, Inc.
      2024   Phase 3   NCT06118255   Belgium;Germany;Italy;Spain;United Kingdom;United States
   University Health Network, Toronto
      2022   Phase 3   NCT05560282   Canada
   University Hospital Antwerp
      2011   Phase 3   EUCTR2011-004114-42-BE   Belgium
   University of California, Los Angeles
      2018   -   NCT04437004   United States
   University of Colorado, Denver
      2024   Phase 4   NCT06598449   United States
Fenfluramine hydrochloride
   YAMAMOTO Hideichiro
      2019   Phase 3   JPRN-jRCT2041200095   Australia;Belgium;Canda;Denmark;France;Germany;Italy;Japan;Korea;Netherland;Norway;Spain;Sweeded;UK;US
   Zogenix International Limited
      2020   Phase 3   EUCTR2019-001331-31-SE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-NL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-DK   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-DE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   JPRN-jRCT2080224792   Australia;Europe;Japan
      2019   Phase 3   EUCTR2019-001331-31-IT   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-GB   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-FR   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-ES   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-BE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-002804-14-NL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-002804-14-IT   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-GB   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-ES   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-DE   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-GB   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-ES   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Norway;Spain;Sweden;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-DK   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-BE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-000474-38-NL   Germany;Netherlands;Spain;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-SE   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-GB   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-ES   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-DK   Australia;Belgium;Denmark;France;Germany;Italy;Japan;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-DE   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-BE   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      -   Phase 3   EUCTR2019-001331-31-PL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      -   Phase 3   EUCTR2016-002804-14-FR   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      -   Phase 3   EUCTR2015-004167-37-NO   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      -   Phase 3   EUCTR2015-004167-37-FR   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2017   Phase 3   NCT03299842   United States
      2017   Phase 3   NCT02926898   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   NCT02823145   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2016   Phase 3   NCT02682927   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Spain;United Kingdom;United States
   Zogenix International Limited, a wholly owned subsidiary of Zogenix Inc.
      2016   Phase 3   EUCTR2016-002804-14-DE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
   Zogenix, Inc.
      2019   Phase 3   NCT03936777   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   -   NCT03780127   -
Frisium*30CPS 10MG
   ISTITUTO C. MONDINO
      2007   -   EUCTR2007-003702-95-IT   Italy
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
Gaba blood level
   Cook Children's Health Care System
      2022   -   NCT05651204   United States
GWP42003-P
   GW Research Ltd
      2015   Phase 3   NCT02224573   -
      2015   Phase 3   EUCTR2014-002939-34-NL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-002939-34-ES   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-PL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-NL   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-GB   Australia;France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-FR   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   Phase 3   EUCTR2014-001834-27-ES   France;Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2015   -   EUCTR2014-000995-24-PL   France;Poland;United Kingdom;United States
      2014   Phase 3   EUCTR2014-002939-34-GB   Israel;Netherlands;Poland;Spain;United Kingdom;United States
      2014   Phase 2;Phase 3   EUCTR2014-000995-24-GB   France;Poland;United Kingdom;United States
      -   Phase 3   EUCTR2014-002939-34-PL   Australia;Israel;Netherlands;Poland;Spain;United Kingdom;United States
   Jazz Pharmaceuticals
      2021   Phase 3   NCT04485104   Italy;Spain;United States
      2015   Phase 3   NCT02224703   Australia;Israel;Netherlands;Poland;Spain;United States
GWP42003-P 10 MG/KG/DAY dose
   Jazz Pharmaceuticals
      2014   Phase 2   NCT02091206   United Kingdom;United States
GWP42003-P 20 MG/KG/DAY dose
   Jazz Pharmaceuticals
      2015   Phase 3   NCT02091375   France;Poland;United Kingdom;United States
      2014   Phase 2   NCT02091206   United Kingdom;United States
GWP42003-P 5 MG/KG/DAY dose
   Jazz Pharmaceuticals
      2014   Phase 2   NCT02091206   United Kingdom;United States
Levodopa
   Natsume Jun
      2020   Phase 4   JPRN-jRCTs041190116   -
Lorcaserin
   Eisai Inc.
      2021   -   NCT04457687   Canada;United States
      2020   Phase 3   NCT04572243   Canada;United States
LP352
   Longboard Pharmaceuticals
      2024   Phase 3   NCT06660394   Australia;Belgium;Brazil;Canada;China;France;Germany;Italy;Latvia;Mexico;Netherlands;Portugal;Serbia;Spain;United Kingdom;United States
      2024   -   NCT06149663   Australia;United States
      2022   Phase 1/Phase 2   NCT05364021   Australia;United States
LP352, bexicaserin
   Longboard Pharmaceuticals
      2022   Phase 2   NCT05626634   Australia;United States
MIC
   Nonomura Hidenori
      2022   Phase 3   JPRN-jRCT2051210182   Australia;Belgium;Canada;China;France;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russia;Serbia;Spain;USA;Ukraine;United Kingdom
      2021   Phase 3   JPRN-jRCT2051210074   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russia;Serbia;Spain;Ukraine;United Kingdom;United States
Multiple
   University of Oxford
      2023   -   NCT05140122   -
None AT this time
   Takeda Development Center Americas, Inc.
      2019   Phase 2   EUCTR2018-002484-25-PT   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      2019   Phase 2   EUCTR2018-002484-25-PL   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
Other antiepileptics
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
Soticlestat
   Nonomura Hidenori
      2022   Phase 3   JPRN-jRCT2051210182   Australia;Belgium;Canada;China;France;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russia;Serbia;Spain;USA;Ukraine;United Kingdom
      2021   Phase 3   JPRN-jRCT2051210074   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russia;Serbia;Spain;Ukraine;United Kingdom;United States
   TAKEDA DEVELOPMENT CENTER AMERICAS INC.
      2022   Phase 3   EUCTR2021-002482-17-IT   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-IT   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
   Takeda
      2024   Phase 3   NCT06422377   Denmark;United Kingdom
      2022   Phase 3   NCT05163314   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   NCT04940624   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2018   Phase 2   NCT03635073   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
   Takeda Development Center America, Inc.
      -   Phase 2   EUCTR2022-001315-44-Outside-EU/EEA   United States
   Takeda Development Center Americas, Inc
      2023   Phase 3   EUCTR2021-002482-17-DE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-PL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-NL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-LV   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-HU   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-GR   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain
      2022   Phase 3   EUCTR2021-002482-17-ES   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-BE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      -   Phase 3   EUCTR2021-002480-22-Outside-EU/EEA   Australia;Brazil;Canada;China;Japan;Latvia;Russian Federation;Serbia;Ukraine;United States
   Takeda Development Center Americas, Inc.
      2023   Phase 3   EUCTR2021-002480-22-DE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-PL   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-NL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-LV   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-HU   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-GR   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-ES   Australia;Belgium;Canada;China;France;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-BE   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2019   Phase 2   EUCTR2018-002485-39-PT   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      2019   Phase 2   EUCTR2018-002485-39-PL   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      -   Phase 3   EUCTR2021-002480-22-FR   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
Stiripentol
   Children's Hospital Medical Center, Cincinnati
      2013   -   NCT01983722   United States
   Cook Children's Health Care System
      2014   -   NCT02239276   United States
   Mayo Clinic
      2012   Phase 4   NCT01533506   United States
   Meiji Seika Pharma Co., Ltd.
      2012   -   JPRN-jRCT1080225085   Japan
   Meiji Seika Pharma Co., Ltd. (formerly MEIJI SEIKA KAISHA Co., LTD.)
      2010   Phase 3   JPRN-jRCT2080221082   -
   University of Colorado, Denver
      2013   -   NCT01835314   United States
   Yushi InoueNational Epilepsy Center, Shizuoka Institute of Epilepsy and Neurological Disorders
      2007   -   JPRN-jRCT1091220014   Japan
Stiripentolo
   ISTITUTO C. MONDINO
      2007   -   EUCTR2007-003702-95-IT   Italy
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
STK-001
   Stoke Therapeutics, Inc
      2021   Phase 2   NCT04740476   United States
STK-001 - multiple ascending doses
   Stoke Therapeutics, Inc
      2020   Phase 1/Phase 2   NCT04442295   United States
STK-001 - single ascending doses
   Stoke Therapeutics, Inc
      2020   Phase 1/Phase 2   NCT04442295   United States
TAK-935
   TAKEDA DEVELOPMENT CENTER AMERICAS INC.
      2022   Phase 3   EUCTR2021-002482-17-IT   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-IT   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
   Takeda
      2018   Phase 2   NCT03650452   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
   Takeda Development Center America, Inc.
      -   Phase 2   EUCTR2022-001315-44-Outside-EU/EEA   United States
   Takeda Development Center Americas, Inc
      2023   Phase 3   EUCTR2021-002482-17-DE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-PL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-NL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-LV   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-HU   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-GR   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain
      2022   Phase 3   EUCTR2021-002482-17-ES   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2022   Phase 3   EUCTR2021-002482-17-BE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      -   Phase 3   EUCTR2021-002480-22-Outside-EU/EEA   Australia;Brazil;Canada;China;Japan;Latvia;Russian Federation;Serbia;Ukraine;United States
   Takeda Development Center Americas, Inc.
      2023   Phase 3   EUCTR2021-002480-22-DE   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-PL   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-NL   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-LV   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-HU   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-GR   Australia;Belgium;Brazil;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Mexico;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United States
      2021   Phase 3   EUCTR2021-002480-22-ES   Australia;Belgium;Canada;China;France;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2021   Phase 3   EUCTR2021-002480-22-BE   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
      2019   Phase 2   EUCTR2018-002485-39-PT   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      2019   Phase 2   EUCTR2018-002485-39-PL   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      2019   Phase 2   EUCTR2018-002484-25-PT   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      2019   Phase 2   EUCTR2018-002484-25-PL   Australia;Canada;China;Israel;Poland;Portugal;Spain;United States
      -   Phase 3   EUCTR2021-002480-22-FR   Australia;Belgium;Canada;China;France;Germany;Greece;Hungary;Italy;Japan;Latvia;Netherlands;Poland;Russian Federation;Serbia;Spain;Ukraine;United Kingdom;United States
Topamax
   ISTITUTO C. MONDINO
      2007   -   EUCTR2007-003702-95-IT   Italy
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
Topiramate
   ISTITUTO C. MONDINO
      2007   -   EUCTR2007-003702-95-IT   Italy
   Inserm-ISP Pole Recherches cliniques et thérapeutiques
      2007   -   EUCTR2007-002198-30-IT   Italy
Turmeric
   NYU Langone Health
      2018   -   NCT03254680   United States
Verapamil
   Gillette Children's Specialty Healthcare
      2012   Phase 2   NCT01607073   United States
Zorevunersen
   Stoke Therapeutics, Inc
      2025   Phase 3   NCT06872125   -
ZX008
   YAMAMOTO Hideichiro
      2019   Phase 3   JPRN-jRCT2041200095   Australia;Belgium;Canda;Denmark;France;Germany;Italy;Japan;Korea;Netherland;Norway;Spain;Sweeded;UK;US
   ZOGENIX INTERNATIONAL LTD
      2016   Phase 3   EUCTR2015-004167-37-IT   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
   Zogenix International Limited
      2020   Phase 3   EUCTR2019-001331-31-SE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-NL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-DK   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2020   Phase 3   EUCTR2019-001331-31-DE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   JPRN-jRCT2080224792   Australia;Europe;Japan
      2019   Phase 3   EUCTR2019-001331-31-IT   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-GB   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-FR   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-ES   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2019   Phase 3   EUCTR2019-001331-31-BE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-002804-14-NL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-002804-14-IT   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-GB   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-ES   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2017   Phase 3   EUCTR2016-000474-38-DE   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-GB   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-ES   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Norway;Spain;Sweden;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-DK   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-002804-14-BE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   EUCTR2016-000474-38-NL   Germany;Netherlands;Spain;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-SE   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-GB   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-ES   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-DK   Australia;Belgium;Denmark;France;Germany;Italy;Japan;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-DE   Australia;Belgium;Denmark;France;Germany;Italy;Norway;Spain;Sweden;Switzerland;United Kingdom
      2016   Phase 3   EUCTR2015-004167-37-BE   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      -   Phase 3   EUCTR2019-001331-31-PL   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
      -   Phase 3   EUCTR2016-002804-14-FR   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      -   Phase 3   EUCTR2015-004167-37-NO   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
      -   Phase 3   EUCTR2015-004167-37-FR   Australia;Belgium;Denmark;France;Germany;Italy;Korea, Republic of;Norway;Spain;Sweden;Switzerland;United Kingdom
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2017   Phase 3   NCT03299842   United States
      2017   Phase 3   NCT02926898   Canada;France;Germany;Netherlands;Spain;United Kingdom;United States
      2016   Phase 3   NCT02823145   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
      2016   Phase 3   NCT02682927   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Japan;Spain;United Kingdom;United States
   Zogenix International Limited, a wholly owned subsidiary of Zogenix Inc.
      2016   Phase 3   EUCTR2016-002804-14-DE   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Netherlands;Norway;Spain;Sweden;United Kingdom;United States
   Zogenix, Inc.
      2019   Phase 3   NCT03936777   Australia;Belgium;Canada;Denmark;France;Germany;Italy;Mexico;Netherlands;Poland;Spain;Sweden;United Kingdom;United States
ZX008 - 0.2 MG/KG/DAY
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2016   Phase 3   NCT02826863   Australia;Belgium;Denmark;France;Germany;Italy;Japan;Norway;Spain;Sweden;United Kingdom
ZX008 - 0.8 MG/KG/DAY
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2016   Phase 3   NCT02826863   Australia;Belgium;Denmark;France;Germany;Italy;Japan;Norway;Spain;Sweden;United Kingdom
ZX008 0.2 TO 0.8 MG/KG/DAY
   Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.
      2018   Phase 1   NCT03467113   United States