164. 眼皮膚白皮症 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 16 / 薬物数 : 44 - (DrugBank : 27) / 標的遺伝子数 : 30 - 標的パスウェイ数 : 137
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
6-mercaptopurine
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Abatacept
Emory University
2014 Phase 1 NCT01917708 United States
Adalimumab
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Alefacept
Emory University
2010 - NCT01319851 United States
Alemtuzumab 0.2 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Alemtuzumab 0.3 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Allogeneic bone marrow transplantation
Fairview University Medical Center
2000 - NCT00006054 United States
Allogeneic hematopoietic stem cell transplantation
Fairview University Medical Center
2000 - NCT00006056 United States
ANTI-thymocyte globulin
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Blood parameters
Assistance Publique - Hôpitaux de Paris
2024 - NCT06138509 France
Busulfan
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Campath 1H
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Corticosteroids
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Cyclophosphamide
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Cyclosporin A
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Cyclosporine
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Dosage OF serotonin and metabolites
Assistance Publique - Hôpitaux de Paris
2024 - NCT06138509 France
Erythromycin
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Etoposide
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Filgrastim
Fairview University Medical Center
2000 - NCT00006056 United States
Fludarabine
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Fludarabine phosphate 30 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Fludarabine phosphate 40 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Infliximab
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Levodopa/carbidopa
University of Wisconsin, Madison
2012 Phase 2 NCT01663935 United States
Losartan
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Lutein plus zeaxanthin
Johns Hopkins University
2014 - NCT02200263 United States
Melphalan
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
2002 Phase 2 NCT00176865 United States
Mesalamine
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Mesna
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Methotrexate
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Methylprednisolone
Fairview University Medical Center
2000 - NCT00006054 United States
Mycophenolate mofetil
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Myeloablative conditioning regimen
Masonic Cancer Center, University of Minnesota
2000 Phase 2/Phase 3 NCT00176826 United States
N-acetylcysteine
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Nitisinone
National Eye Institute (NEI)
2013 Phase 1/Phase 2 NCT01838655 United States
Pirfenidone
Jesse Roman
2019 Phase 2 NCT04193592 Puerto Rico;United States
William Gahl, M.D.
2005 Phase 2 NCT00001596 Puerto Rico;United States
Pravastatin
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Prednisone
Fairview University Medical Center
2000 - NCT00006054 United States
Stem cell transplant
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
2000 Phase 2/Phase 3 NCT00176826 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Tacrolimus
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Transplant preparative regimen OF alemtuzumab, fludarabine, thiotepa, and melphalan
Washington University School of Medicine
2013 Phase 2 NCT01821781 United States
Zileuton
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Abatacept
Emory University
2014 Phase 1 NCT01917708 United States
Adalimumab
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Alefacept
Emory University
2010 - NCT01319851 United States
Alemtuzumab 0.2 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Alemtuzumab 0.3 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Allogeneic bone marrow transplantation
Fairview University Medical Center
2000 - NCT00006054 United States
Allogeneic hematopoietic stem cell transplantation
Fairview University Medical Center
2000 - NCT00006056 United States
ANTI-thymocyte globulin
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Blood parameters
Assistance Publique - Hôpitaux de Paris
2024 - NCT06138509 France
Busulfan
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Campath 1H
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Corticosteroids
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Cyclophosphamide
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Cyclosporin A
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Cyclosporine
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Dosage OF serotonin and metabolites
Assistance Publique - Hôpitaux de Paris
2024 - NCT06138509 France
Erythromycin
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Etoposide
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Filgrastim
Fairview University Medical Center
2000 - NCT00006056 United States
Fludarabine
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Fludarabine phosphate 30 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Fludarabine phosphate 40 MG
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Infliximab
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Levodopa/carbidopa
University of Wisconsin, Madison
2012 Phase 2 NCT01663935 United States
Losartan
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Lutein plus zeaxanthin
Johns Hopkins University
2014 - NCT02200263 United States
Melphalan
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
2002 Phase 2 NCT00176865 United States
Mesalamine
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Mesna
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Methotrexate
Fairview University Medical Center
2000 - NCT00006056 United States
2000 - NCT00006054 United States
Methylprednisolone
Fairview University Medical Center
2000 - NCT00006054 United States
Mycophenolate mofetil
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
Myeloablative conditioning regimen
Masonic Cancer Center, University of Minnesota
2000 Phase 2/Phase 3 NCT00176826 United States
N-acetylcysteine
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Nitisinone
National Eye Institute (NEI)
2013 Phase 1/Phase 2 NCT01838655 United States
Pirfenidone
Jesse Roman
2019 Phase 2 NCT04193592 Puerto Rico;United States
William Gahl, M.D.
2005 Phase 2 NCT00001596 Puerto Rico;United States
Pravastatin
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States
Prednisone
Fairview University Medical Center
2000 - NCT00006054 United States
Stem cell transplant
Masonic Cancer Center, University of Minnesota
2002 Phase 2 NCT00176865 United States
2000 Phase 2/Phase 3 NCT00176826 United States
Stem cell transplantation
Masonic Cancer Center, University of Minnesota
2012 - NCT01652092 United States
Tacrolimus
National Institute of Allergy and Infectious Diseases (NIAID)
2007 Phase 2 NCT00514982 United States
Transplant preparative regimen OF alemtuzumab, fludarabine, thiotepa, and melphalan
Washington University School of Medicine
2013 Phase 2 NCT01821781 United States
Zileuton
National Human Genome Research Institute (NHGRI)
2007 Phase 1/Phase 2 NCT00467831 United States