171. ウィルソン病 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 86 / 薬物数 : 68 - (DrugBank : 16) / 標的遺伝子数 : 7 - 標的パスウェイ数 : 33
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
24 hour copper IN urine and liver function test
Assiut University
2024 - NCT05792319 -
64cucl2
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
900MG teta 4HCL once daily formulation
Orphalan
2024 Phase 1 NCT06128954 United Kingdom
Adeno-associated viral vector serotype 3B encoding shortened human ATP7B
Vivet Therapeutics SAS
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DK Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DE Denmark;Germany;United Kingdom;United States
Adeno-associated viral vector serotype 9 encoding human ATP7B
Ultragenyx Pharmaceutical Inc.
2023 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-PT Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
2022 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-ES Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
Allogeneic mesenchymal stem cell transplantation
Murat Kantarcioglu
2011 - NCT01378182 Turkey
ALXN1840
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
Alexion
2023 - NCT05686564 -
Alexion Pharmaceuticals
2020 Phase 1 NCT04526210 United States
2020 Phase 1 NCT04526197 United States
2014 Phase 2 NCT02273596 Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2021 Phase 2 EUCTR2019-003711-60-DE Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-GB Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-FR Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-DK Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-AT Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2021 Phase 3 NCT05047523 Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
2020 Phase 2 NCT04573309 New Zealand;United Kingdom;United States
2020 Phase 2 EUCTR2020-001104-41-GB United Kingdom
2019 Phase 1 NCT05641311 United Kingdom
2018 Phase 3 NCT03403205 Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Artamin 150 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Artamin 250 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
BIS-choline tetrathiomolybdate
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, INC.
2014 Phase 2 EUCTR2014-001703-41-DE Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals, Inc
2021 Phase 2 EUCTR2019-003711-60-DE Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-GB Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-FR Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-DK Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-AT Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2020 Phase 2 NCT04422431 Australia;Austria;Belgium;Canada;Denmark;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Singapore;Spain;United Kingdom;United States
2020 Phase 2 EUCTR2020-001104-41-GB United Kingdom
2014 Phase 2 EUCTR2014-001703-41-AT Austria;Germany;Poland;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2015 Phase 2 EUCTR2014-001703-41-GB Austria;Germany;Poland;United Kingdom;United States
2014 Phase 2 EUCTR2014-001703-41-PL Austria;Germany;Poland;United Kingdom;United States
BIS-choline tetrathiomolybdate, BIS[(2-hydroxyethyl)trimethylammonium] tetrathiomolybdate
Alexion Pharmaceuticals, Inc.
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Botulinum toxin type A
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2016 - NCT06762509 China
Bupropion hydrochloride
Alexion Pharmaceuticals
2020 Phase 1 NCT04526210 United States
Celecoxib
Alexion Pharmaceuticals
2020 Phase 1 NCT04526197 United States
Copper
Anhui Provincial Hospital
2017 - ChiCTR-DDD-17010552 China
First Affiliated Hospital of Sun Yat-Sen University
2020 - ChiCTR2200057544 China
Shanghai Tongren Hospital
2019 Phase 0 ChiCTR1900023410 China
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2023 Phase 1 ChiCTR2500098794 China
Copper (64CU) chloride
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
Cufence
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Cuprior
Orphalan
2024 Phase 1 NCT06128954 United Kingdom
Cuprior 150 MG
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Cuprior 150 MG FILM-coated tablets
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Cuprior 150MG FILM-coated tablets
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine 150MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine 250 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Dexmedetomidine
The First Affiliated Hospital of Anhui University of Chinese Medicine
2021 Phase 0 ChiCTR2100050549 China
Dmps
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
Dmsa
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
Fibroscan
University of Aarhus
2016 - NCT02702765 Denmark
Functional hepatic nitrogen clearance
University of Aarhus
2016 - NCT02702765 Denmark
Galactose
University of Aarhus
2016 - NCT02702765 Denmark
Gandouling
Jun Li
2023 Phase 4 NCT05305872 China
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2023 Phase 1 ChiCTR2500098794 China
2021 Phase 0 ChiCTR2100053629 China
Imaging and fluid biomarkers
University College, London
2018 - NCT04212195 United Kingdom
Intravenous LY-M003
Chaohui Yu
2024 Early Phase 1 NCT06650319 China
Liver biopsy
University of Aarhus
2016 - NCT02702765 Denmark
LOW copper diet
Second Affiliated Hospital, School of Medicine, Zhejiang University
2004 - NCT04965545 China
Metalcaptase
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Metalcaptase® 150 MG gastro-resistant tablet
Orphalan
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Metalcaptase® 300 MG gastro-resistant tablet
Orphalan
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
MWAV201
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
2024 - NCT06663878 China
Next generation sequencing
University College, London
2018 - NCT04212195 United Kingdom
NPC-02
Nobelpharma
2005 Phase 3 NCT00212355 -
Once A DAY trientine
Yale University
2010 - NCT01472874 United States
Pemine - 150 MG capsule rigide 50 capsule
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Penicillamine
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Orphalan
2018 Phase 3 NCT03539952 Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
The First Affiliated Hospital, Sun Yat-Sen University
2022 Phase 1 ChiCTR2200058434 China
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Plasma exchange
Institute of Liver and Biliary Sciences, India
2024 - NCT06698991 India
SOC therapy
Alexion Pharmaceuticals, Inc.
2018 Phase 3 NCT03403205 Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Taiwan;Turkey;United Kingdom;United States
Standard medical treatment
Institute of Liver and Biliary Sciences, India
2024 - NCT06698991 India
Standard OF care medications
Alexion Pharmaceuticals
2016 - NCT02763215 Austria;Germany;Poland;United Kingdom;United States
Teta 4HCL
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2018 Phase 3 NCT03539952 Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Teta.4HCI
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Teta.4HCL
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Tetrathiomolybdate
National Center for Research Resources (NCRR)
1994 Phase 3 NCT00004339 United States
Tiomolibdic acid
Alexion Pharmaceuticals, Inc
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Trientine
Excelsior
2018 - NCT03299829 Taiwan
National Center for Research Resources (NCRR)
1994 Phase 3 NCT00004339 United States
Trientine dihydrochloride
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Univar BV
2016 Phase 4 NCT02426905 Germany;Greece;Italy;United Kingdom
2013 Phase 1 NCT01874028 Germany
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
Trientine dihydrochloride 300MG capsules
UNIVAR LTD
2016 Phase 2 EUCTR2013-003564-31-IT France;Germany;Greece;Italy;Spain;United Kingdom
Univar B.V.
2014 Phase 4 EUCTR2013-003564-31-DE Germany;Italy
Trientine tetrahydrochloride
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Triethylenetetramine dihydrochloride
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Ultrasound
University of Aarhus
2016 - NCT02702765 Denmark
UX701
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04884815 Canada;Portugal;Spain;United Kingdom;United States
Ultragenyx Pharmaceutical Inc.
2023 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-PT Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
2022 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-ES Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
VTX-801
Vivet Therapeutics SAS
2021 Phase 1/Phase 2 NCT04537377 Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DK Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DE Denmark;Germany;United Kingdom;United States
Wilzin
Alexion Pharmaceuticals, Inc
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
WTX101
Alexion Pharmaceuticals, INC.
2014 Phase 2 EUCTR2014-001703-41-DE Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2014 Phase 2 EUCTR2014-001703-41-AT Austria;Germany;Poland;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2015 Phase 2 EUCTR2014-001703-41-GB Austria;Germany;Poland;United Kingdom;United States
2014 Phase 2 EUCTR2014-001703-41-PL Austria;Germany;Poland;United Kingdom;United States
Zinc
Prof. Elon Pras
2018 - NCT03659331 -
The First Affiliated Hospital, Sun Yat-Sen University
2022 Phase 1 ChiCTR2200058434 China
Zinc acetate
National Center for Research Resources (NCRR)
1993 Phase 4 NCT00004338 United States
Nobelpharma
2004 Phase 3 NCT00212368 -
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
Zinc acetate dihydrate
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
Zinc gluconate
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2021 Phase 0 ChiCTR2100053629 China
Zink natur-drogeriet
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
Assiut University
2024 - NCT05792319 -
64cucl2
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
900MG teta 4HCL once daily formulation
Orphalan
2024 Phase 1 NCT06128954 United Kingdom
Adeno-associated viral vector serotype 3B encoding shortened human ATP7B
Vivet Therapeutics SAS
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DK Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DE Denmark;Germany;United Kingdom;United States
Adeno-associated viral vector serotype 9 encoding human ATP7B
Ultragenyx Pharmaceutical Inc.
2023 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-PT Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
2022 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-ES Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
Allogeneic mesenchymal stem cell transplantation
Murat Kantarcioglu
2011 - NCT01378182 Turkey
ALXN1840
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
Alexion
2023 - NCT05686564 -
Alexion Pharmaceuticals
2020 Phase 1 NCT04526210 United States
2020 Phase 1 NCT04526197 United States
2014 Phase 2 NCT02273596 Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2021 Phase 2 EUCTR2019-003711-60-DE Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-GB Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-FR Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-DK Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-AT Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2021 Phase 3 NCT05047523 Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
2020 Phase 2 NCT04573309 New Zealand;United Kingdom;United States
2020 Phase 2 EUCTR2020-001104-41-GB United Kingdom
2019 Phase 1 NCT05641311 United Kingdom
2018 Phase 3 NCT03403205 Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Artamin 150 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Artamin 250 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
BIS-choline tetrathiomolybdate
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, INC.
2014 Phase 2 EUCTR2014-001703-41-DE Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals, Inc
2021 Phase 2 EUCTR2019-003711-60-DE Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-GB Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-FR Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-DK Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 2 EUCTR2019-003711-60-AT Australia;Austria;Belgium;Canada;Denmark;France;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Sweden;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2020 Phase 2 NCT04422431 Australia;Austria;Belgium;Canada;Denmark;Germany;Korea, Republic of;New Zealand;Poland;Russian Federation;Singapore;Spain;United Kingdom;United States
2020 Phase 2 EUCTR2020-001104-41-GB United Kingdom
2014 Phase 2 EUCTR2014-001703-41-AT Austria;Germany;Poland;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2015 Phase 2 EUCTR2014-001703-41-GB Austria;Germany;Poland;United Kingdom;United States
2014 Phase 2 EUCTR2014-001703-41-PL Austria;Germany;Poland;United Kingdom;United States
BIS-choline tetrathiomolybdate, BIS[(2-hydroxyethyl)trimethylammonium] tetrathiomolybdate
Alexion Pharmaceuticals, Inc.
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Botulinum toxin type A
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2016 - NCT06762509 China
Bupropion hydrochloride
Alexion Pharmaceuticals
2020 Phase 1 NCT04526210 United States
Celecoxib
Alexion Pharmaceuticals
2020 Phase 1 NCT04526197 United States
Copper
Anhui Provincial Hospital
2017 - ChiCTR-DDD-17010552 China
First Affiliated Hospital of Sun Yat-Sen University
2020 - ChiCTR2200057544 China
Shanghai Tongren Hospital
2019 Phase 0 ChiCTR1900023410 China
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2023 Phase 1 ChiCTR2500098794 China
Copper (64CU) chloride
Aarhus University Hospital
2021 Phase 2 EUCTR2021-000102-25-DK Denmark
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
Cufence
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Cuprior
Orphalan
2024 Phase 1 NCT06128954 United Kingdom
Cuprior 150 MG
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Cuprior 150 MG FILM-coated tablets
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Cuprior 150MG FILM-coated tablets
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine 150MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
D-penicillamine 250 MG
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Dexmedetomidine
The First Affiliated Hospital of Anhui University of Chinese Medicine
2021 Phase 0 ChiCTR2100050549 China
Dmps
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
Dmsa
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
Fibroscan
University of Aarhus
2016 - NCT02702765 Denmark
Functional hepatic nitrogen clearance
University of Aarhus
2016 - NCT02702765 Denmark
Galactose
University of Aarhus
2016 - NCT02702765 Denmark
Gandouling
Jun Li
2023 Phase 4 NCT05305872 China
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2023 Phase 1 ChiCTR2500098794 China
2021 Phase 0 ChiCTR2100053629 China
Imaging and fluid biomarkers
University College, London
2018 - NCT04212195 United Kingdom
Intravenous LY-M003
Chaohui Yu
2024 Early Phase 1 NCT06650319 China
Liver biopsy
University of Aarhus
2016 - NCT02702765 Denmark
LOW copper diet
Second Affiliated Hospital, School of Medicine, Zhejiang University
2004 - NCT04965545 China
Metalcaptase
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Metalcaptase® 150 MG gastro-resistant tablet
Orphalan
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Metalcaptase® 300 MG gastro-resistant tablet
Orphalan
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
MWAV201
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
2024 - NCT06663878 China
Next generation sequencing
University College, London
2018 - NCT04212195 United Kingdom
NPC-02
Nobelpharma
2005 Phase 3 NCT00212355 -
Once A DAY trientine
Yale University
2010 - NCT01472874 United States
Pemine - 150 MG capsule rigide 50 capsule
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Penicillamine
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Orphalan
2018 Phase 3 NCT03539952 Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
The First Affiliated Hospital, Sun Yat-Sen University
2022 Phase 1 ChiCTR2200058434 China
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Plasma exchange
Institute of Liver and Biliary Sciences, India
2024 - NCT06698991 India
SOC therapy
Alexion Pharmaceuticals, Inc.
2018 Phase 3 NCT03403205 Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;New Zealand;Poland;Russian Federation;Serbia;Singapore;Spain;Taiwan;Turkey;United Kingdom;United States
Standard medical treatment
Institute of Liver and Biliary Sciences, India
2024 - NCT06698991 India
Standard OF care medications
Alexion Pharmaceuticals
2016 - NCT02763215 Austria;Germany;Poland;United Kingdom;United States
Teta 4HCL
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2018 Phase 3 NCT03539952 Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Teta.4HCI
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Teta.4HCL
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
Tetrathiomolybdate
National Center for Research Resources (NCRR)
1994 Phase 3 NCT00004339 United States
Tiomolibdic acid
Alexion Pharmaceuticals, Inc
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2021 Phase 3 EUCTR2021-001015-82-ES Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
2021 Phase 3 EUCTR2021-001015-82-DE Australia;France;Germany;Japan;Korea, Republic of;Poland;Spain;United Kingdom
- Phase 3 EUCTR2021-001015-82-PL Australia;Austria;Canada;Czechia;Denmark;France;Germany;Hungary;Japan;Korea, Republic of;Netherlands;Poland;Russian Federation;Serbia;Spain;Turkey;United Kingdom;United States
Trientine
Excelsior
2018 - NCT03299829 Taiwan
National Center for Research Resources (NCRR)
1994 Phase 3 NCT00004339 United States
Trientine dihydrochloride
Alexion Pharmaceuticals Inc.
2021 Phase 2 EUCTR2020-005832-31-DK Denmark
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Univar BV
2016 Phase 4 NCT02426905 Germany;Greece;Italy;United Kingdom
2013 Phase 1 NCT01874028 Germany
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
Trientine dihydrochloride 300MG capsules
UNIVAR LTD
2016 Phase 2 EUCTR2013-003564-31-IT France;Germany;Greece;Italy;Spain;United Kingdom
Univar B.V.
2014 Phase 4 EUCTR2013-003564-31-DE Germany;Italy
Trientine tetrahydrochloride
GMP ORPHAN SA
2017 Phase 3 EUCTR2016-003876-29-IT Austria;Brazil;Denmark;France;Germany;Italy;Micronesia, Federated States of;Poland;United Kingdom;United States
Orphalan
2019 Phase 3 EUCTR2016-003876-29-BE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DK Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-DE Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
gmp-orphan SA
2017 Phase 3 EUCTR2016-003876-29-GB Austria;Belgium;Brazil;Denmark;France;Germany;Italy;Poland;Sweden;United Kingdom;United States
2017 Phase 3 EUCTR2016-003876-29-AT Austria;Brazil;Denmark;France;Germany;Italy;Poland;United Kingdom
Triethylenetetramine dihydrochloride
Univar Solutions, B.V.
2021 Phase 4 EUCTR2020-004604-33-PL Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-FR Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DK Denmark;France;Germany;Poland
2021 Phase 4 EUCTR2020-004604-33-DE Denmark;France;Germany;Poland
Ultrasound
University of Aarhus
2016 - NCT02702765 Denmark
UX701
Ultragenyx Pharmaceutical Inc
2021 Phase 1/Phase 2 NCT04884815 Canada;Portugal;Spain;United Kingdom;United States
Ultragenyx Pharmaceutical Inc.
2023 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-PT Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
2022 Phase 1;Phase 2;Phase 3 EUCTR2020-005266-34-ES Argentina;Austria;Brazil;Canada;France;Germany;Italy;Japan;Poland;Portugal;Spain;United Kingdom;United States
VTX-801
Vivet Therapeutics SAS
2021 Phase 1/Phase 2 NCT04537377 Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DK Denmark;Germany;United Kingdom;United States
2021 Phase 1;Phase 2 EUCTR2020-000963-22-DE Denmark;Germany;United Kingdom;United States
Wilzin
Alexion Pharmaceuticals, Inc
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
WTX101
Alexion Pharmaceuticals, INC.
2014 Phase 2 EUCTR2014-001703-41-DE Austria;Germany;Poland;United Kingdom;United States
Alexion Pharmaceuticals, Inc.
2014 Phase 2 EUCTR2014-001703-41-AT Austria;Germany;Poland;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2015 Phase 2 EUCTR2014-001703-41-GB Austria;Germany;Poland;United Kingdom;United States
2014 Phase 2 EUCTR2014-001703-41-PL Austria;Germany;Poland;United Kingdom;United States
Zinc
Prof. Elon Pras
2018 - NCT03659331 -
The First Affiliated Hospital, Sun Yat-Sen University
2022 Phase 1 ChiCTR2200058434 China
Zinc acetate
National Center for Research Resources (NCRR)
1993 Phase 4 NCT00004338 United States
Nobelpharma
2004 Phase 3 NCT00212368 -
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
Zinc acetate dihydrate
Alexion Pharmaceuticals, Inc
2020 Phase 3 EUCTR2017-004135-36-PT Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2020 Phase 3 EUCTR2017-004135-36-NL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-SE Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2019 Phase 3 EUCTR2017-004135-36-DK Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-DE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-CZ Australia;Austria;Belgium;Brazil;Canada;Colombia;Czech Republic;Czechia;Denmark;France;Germany;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-AT Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Democratic People's Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-PL Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Czechia;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
- Phase 3 EUCTR2017-004135-36-BE Australia;Austria;Belgium;Brazil;Canada;Colombia;Croatia;Czech Republic;Denmark;France;Germany;Greece;Hong Kong;Hungary;Israel;Italy;Japan;Korea, Republic of;Netherlands;New Zealand;Poland;Portugal;Russian Federation;Serbia;Singapore;Spain;Sweden;Taiwan;Turkey;United Kingdom;United States
Wilson Therapeutics AB
2018 Phase 3 EUCTR2017-004135-36-HU Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-GB Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-FR Austria;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Portugal;Spain;Sweden;United Kingdom;United States
2018 Phase 3 EUCTR2017-004135-36-ES Austria;Czech Republic;France;Germany;Hungary;Israel;Italy;Poland;Spain;United Kingdom;United States
Zinc gluconate
Second Affiliated Hospital, School of Medicine, Zhejiang University
2019 Early Phase 1 NCT03957720 China
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark
The First Affiliated Hospital of Anhui University of Traditional Chinese Medicine
2021 Phase 0 ChiCTR2100053629 China
Zink natur-drogeriet
The Department of Hepatology and Gastroenterology, Aarhus University Hospital
2019 Phase 4 EUCTR2019-000905-57-DK Denmark