215. ファロー四徴症 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 24 / 薬物数 : 32 - (DrugBank : 17) / 標的遺伝子数 : 15 - 標的パスウェイ数 : 48
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Brain natriuretic peptide
Shanghai Jiao Tong University School of Medicine
2013 - NCT01941576 China
Calcium gluconate
National Center for Research Resources (NCRR)
1995 - NCT00004361 -
Cardiac MRI
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Cellvizio 100 series system with confocal miniprobes
Aditya Kaza
2019 Phase 2 NCT04017975 United States
Coenzyme Q10
Fuwai Central China Cardiovascualr Hospital
2019 Phase 0 ChiCTR1900025513 China
Cold cadioplegia
Ain Shams University
2021 Early Phase 1 NCT05176782 Egypt
Dapagliflozin
The University of Hong Kong
2025 Phase 4 NCT06668389 Hong Kong
Dexmedetomidine
Athena Zuppa
2004 Phase 1 NCT00573066 -
HealthCore-NERI
2014 Phase 1 NCT01915277 United States
Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
2016 - ChiCTR-IOR-16008571 China
Dexmedetomidine HCL 100 MCG/ML INJ
National Cardiovascular Center Harapan Kita Hospital Indonesia
2022 Phase 2/Phase 3 NCT05579964 Indonesia
Dobutamin
Competence Network for Congenital Heart Defects
2007 Phase 3 NCT00564993 Germany
Dobutamine
Deutsche Herzzentrum Berlin, Kompetenznetz Angeborene Herzfehler
2007 - EUCTR2007-003461-41-DE Germany
University Hospital Tuebingen
2007 - NCT00557934 Germany
Echocardiogram
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Entresto pill
Mayo Clinic
2025 Phase 3 NCT06693674 United States
Eplerenone
Washington University School of Medicine
2013 Phase 4 NCT01971593 United States
Fentanyl (LOW dose) + dexmedetomidine
Nationwide Children's Hospital
2008 Phase 2 NCT00848393 United States
Fluorescite
Aditya Kaza
2019 Phase 2 NCT04017975 United States
Glutamine
Shanghai Children's Hospital
2025 - ChiCTR2500102350 China
HTK cardioplegia
Ain Shams University
2021 Early Phase 1 NCT05176782 Egypt
Ketamine
Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
2016 - ChiCTR-IOR-16008571 China
Losartan
Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)
2013 Phase 2 NCT02010905 Netherlands
Losartan potassium
Academisch medisch centrum
2014 - EUCTR2013-002091-41-NL Netherlands
N-thymidine
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
N15-thymidine
Weill Medical College of Cornell University
2015 - NCT06587165 United States
Physical exam
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Propranolol hydrochloride
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
SGLT2 inhibitors
Leiden University Medical Center
2023 - NCT06932081 Macedonia, The Former Yugoslav Republic of;Netherlands;United Kingdom;United States
Sodium chloride
Shanghai Children's Hospital
2025 - ChiCTR2500102350 China
Shanghai Jiao Tong University School of Medicine
2013 - NCT01941576 China
Sodium citrate
National Center for Research Resources (NCRR)
1995 - NCT00004361 -
Specimen collection
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Sulfur hexafluoride
Nemours Children's Clinic
2022 Phase 1/Phase 2 NCT05186415 United States
Tranexamic acid
National Center for Cardiovascular Diseases, Fuwai Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
2018 - ChiCTR1800019578 China
Urine collection
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Shanghai Jiao Tong University School of Medicine
2013 - NCT01941576 China
Calcium gluconate
National Center for Research Resources (NCRR)
1995 - NCT00004361 -
Cardiac MRI
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Cellvizio 100 series system with confocal miniprobes
Aditya Kaza
2019 Phase 2 NCT04017975 United States
Coenzyme Q10
Fuwai Central China Cardiovascualr Hospital
2019 Phase 0 ChiCTR1900025513 China
Cold cadioplegia
Ain Shams University
2021 Early Phase 1 NCT05176782 Egypt
Dapagliflozin
The University of Hong Kong
2025 Phase 4 NCT06668389 Hong Kong
Dexmedetomidine
Athena Zuppa
2004 Phase 1 NCT00573066 -
HealthCore-NERI
2014 Phase 1 NCT01915277 United States
Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
2016 - ChiCTR-IOR-16008571 China
Dexmedetomidine HCL 100 MCG/ML INJ
National Cardiovascular Center Harapan Kita Hospital Indonesia
2022 Phase 2/Phase 3 NCT05579964 Indonesia
Dobutamin
Competence Network for Congenital Heart Defects
2007 Phase 3 NCT00564993 Germany
Dobutamine
Deutsche Herzzentrum Berlin, Kompetenznetz Angeborene Herzfehler
2007 - EUCTR2007-003461-41-DE Germany
University Hospital Tuebingen
2007 - NCT00557934 Germany
Echocardiogram
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Entresto pill
Mayo Clinic
2025 Phase 3 NCT06693674 United States
Eplerenone
Washington University School of Medicine
2013 Phase 4 NCT01971593 United States
Fentanyl (LOW dose) + dexmedetomidine
Nationwide Children's Hospital
2008 Phase 2 NCT00848393 United States
Fluorescite
Aditya Kaza
2019 Phase 2 NCT04017975 United States
Glutamine
Shanghai Children's Hospital
2025 - ChiCTR2500102350 China
HTK cardioplegia
Ain Shams University
2021 Early Phase 1 NCT05176782 Egypt
Ketamine
Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
2016 - ChiCTR-IOR-16008571 China
Losartan
Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)
2013 Phase 2 NCT02010905 Netherlands
Losartan potassium
Academisch medisch centrum
2014 - EUCTR2013-002091-41-NL Netherlands
N-thymidine
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
N15-thymidine
Weill Medical College of Cornell University
2015 - NCT06587165 United States
Physical exam
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Propranolol hydrochloride
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
SGLT2 inhibitors
Leiden University Medical Center
2023 - NCT06932081 Macedonia, The Former Yugoslav Republic of;Netherlands;United Kingdom;United States
Sodium chloride
Shanghai Children's Hospital
2025 - ChiCTR2500102350 China
Shanghai Jiao Tong University School of Medicine
2013 - NCT01941576 China
Sodium citrate
National Center for Research Resources (NCRR)
1995 - NCT00004361 -
Specimen collection
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States
Sulfur hexafluoride
Nemours Children's Clinic
2022 Phase 1/Phase 2 NCT05186415 United States
Tranexamic acid
National Center for Cardiovascular Diseases, Fuwai Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College
2018 - ChiCTR1800019578 China
Urine collection
Weill Medical College of Cornell University
2022 Phase 1 NCT04713657 United States