255. 複合カルボキシラーゼ欠損症 Disease details / Clinical trials / Drug dev / DR info /


臨床試験数 : 2 / 薬物数 : 7 - (DrugBank : 0) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
ORL-1B
   Orpha Labs
      2013   Phase 1/Phase 2   NCT03269045   -