278. 巨大リンパ管奇形(頚部顔面病変) Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 32 / 薬物数 : 32 - (DrugBank : 12) / 標的遺伝子数 : 8 - 標的パスウェイ数 : 136
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Alpelisib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Novartis Pharmaceuticals
2023 Phase 2/Phase 3 NCT05948943 Australia;Belgium;France;Germany;Italy;Spain;United States
Bleomycin
Fujino Akihiro
2016 - JPRN-jRCTs031180265 -
West China Hospital
2023 Phase 2 NCT06437158 China
CERC-006
Cerecor Inc
2021 Phase 1 NCT04994002 United States
Genetic profiling OF ALL eligible patients
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
2024 - NCT06892964 Italy
Indocyanine green
Aitaro Takimoto
2017 Phase 2 JPRN-jRCTs041190036 -
Nagoya University Graduate School of Medicine
2017 - JPRN-UMIN000025845 Japan
Indocyanine green-guided partial resection and sclerotherapy
Nanjing Children's Hospital
2023 - NCT06275022 China
Inflow occlusion with perforation OF septation and sclerotherapy
Nanjing Children's Hospital
2023 - NCT06275022 China
L04aa10
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
Mirdametinib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
OK432
Richard JH Smith
1998 Phase 4 NCT03427619 United States
Oral sirolimus
Children's Hospital of Fudan University
2021 Phase 4 NCT04921722 China
Percutaneous sirolimus
Children's Hospital of Fudan University
2021 Phase 4 NCT04921722 China
Picibanil
University of Iowa
2000 Phase 2/Phase 3 NCT00010452 United States
Polidocanol
Mori Hiroki
2024 Phase 2 JPRN-jRCTs031230604 Japan;Non
Propranolol
University of Tokyo
2012 Phase 2 JPRN-UMIN000008498 Japan
PTX-022
Palvella Therapeutics, Inc.
2022 Phase 2 NCT05050149 United States
Qtorin 3.9% rapamycin anhydrous GEL
Palvella Therapeutics, Inc.
2024 Phase 3 NCT06239480 United States
Rapamune
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
West China Hospital
2024 Phase 2/Phase 3 NCT06673290 China
RLY-2608
Relay Therapeutics, Inc.
2025 Phase 2 NCT06789913 United States
Sclerotherapy with intralesional bleomycin injection
National Children's Hospital, Vietnam
2018 - NCT06943703 Vietnam
Selenium
Medical College of Wisconsin
2010 Phase 1 NCT01212965 United States
Sildenafil
Beijing Children's Hospital
2014 - ChiCTR-OPC-16008702 China
Sildenafil 20 MG tablets
Stanford University
2015 Phase 2 NCT02335242 United States
Sirolimus
Children's Hospital Medical Center, Cincinnati
2009 Phase 2 NCT00975819 United States
Gifu University
2017 - JPRN-UMIN000030522 Japan
Gifu University Hospital
2020 Phase 3 JPRN-UMIN000038973 Japan
Medical University of South Carolina
2022 Phase 2 NCT04861064 United States
West China Hospital
2024 Phase 2/Phase 3 NCT06673290 China
Sirolimus 0,1% CRèME
CHRU TOURS
2019 Phase 2 EUCTR2018-001359-11-FR France
Sirolimus 1MG oral tablet
Sohag University
2023 - NCT06160739 Egypt
Sirolimus 1MG/ML
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
Sirolimus oral liquid product 1MG/ML
University Hospital, Tours
2020 Phase 2 NCT04128722 France
TARA-002
Protara Therapeutics
2023 Phase 2 NCT05871970 United States
Topical 0.1% sirolimus
University Hospital, Tours
2019 Phase 2 NCT03972592 France
Topical vehicle
University Hospital, Tours
2019 Phase 2 NCT03972592 France
Water
Fujino Akihiro
2016 - JPRN-jRCTs031180265 -
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Novartis Pharmaceuticals
2023 Phase 2/Phase 3 NCT05948943 Australia;Belgium;France;Germany;Italy;Spain;United States
Bleomycin
Fujino Akihiro
2016 - JPRN-jRCTs031180265 -
West China Hospital
2023 Phase 2 NCT06437158 China
CERC-006
Cerecor Inc
2021 Phase 1 NCT04994002 United States
Genetic profiling OF ALL eligible patients
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
2024 - NCT06892964 Italy
Indocyanine green
Aitaro Takimoto
2017 Phase 2 JPRN-jRCTs041190036 -
Nagoya University Graduate School of Medicine
2017 - JPRN-UMIN000025845 Japan
Indocyanine green-guided partial resection and sclerotherapy
Nanjing Children's Hospital
2023 - NCT06275022 China
Inflow occlusion with perforation OF septation and sclerotherapy
Nanjing Children's Hospital
2023 - NCT06275022 China
L04aa10
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
Mirdametinib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
OK432
Richard JH Smith
1998 Phase 4 NCT03427619 United States
Oral sirolimus
Children's Hospital of Fudan University
2021 Phase 4 NCT04921722 China
Percutaneous sirolimus
Children's Hospital of Fudan University
2021 Phase 4 NCT04921722 China
Picibanil
University of Iowa
2000 Phase 2/Phase 3 NCT00010452 United States
Polidocanol
Mori Hiroki
2024 Phase 2 JPRN-jRCTs031230604 Japan;Non
Propranolol
University of Tokyo
2012 Phase 2 JPRN-UMIN000008498 Japan
PTX-022
Palvella Therapeutics, Inc.
2022 Phase 2 NCT05050149 United States
Qtorin 3.9% rapamycin anhydrous GEL
Palvella Therapeutics, Inc.
2024 Phase 3 NCT06239480 United States
Rapamune
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
West China Hospital
2024 Phase 2/Phase 3 NCT06673290 China
RLY-2608
Relay Therapeutics, Inc.
2025 Phase 2 NCT06789913 United States
Sclerotherapy with intralesional bleomycin injection
National Children's Hospital, Vietnam
2018 - NCT06943703 Vietnam
Selenium
Medical College of Wisconsin
2010 Phase 1 NCT01212965 United States
Sildenafil
Beijing Children's Hospital
2014 - ChiCTR-OPC-16008702 China
Sildenafil 20 MG tablets
Stanford University
2015 Phase 2 NCT02335242 United States
Sirolimus
Children's Hospital Medical Center, Cincinnati
2009 Phase 2 NCT00975819 United States
Gifu University
2017 - JPRN-UMIN000030522 Japan
Gifu University Hospital
2020 Phase 3 JPRN-UMIN000038973 Japan
Medical University of South Carolina
2022 Phase 2 NCT04861064 United States
West China Hospital
2024 Phase 2/Phase 3 NCT06673290 China
Sirolimus 0,1% CRèME
CHRU TOURS
2019 Phase 2 EUCTR2018-001359-11-FR France
Sirolimus 1MG oral tablet
Sohag University
2023 - NCT06160739 Egypt
Sirolimus 1MG/ML
CHRU TOURS
2019 Phase 2 EUCTR2019-001530-33-FR France
Sirolimus oral liquid product 1MG/ML
University Hospital, Tours
2020 Phase 2 NCT04128722 France
TARA-002
Protara Therapeutics
2023 Phase 2 NCT05871970 United States
Topical 0.1% sirolimus
University Hospital, Tours
2019 Phase 2 NCT03972592 France
Topical vehicle
University Hospital, Tours
2019 Phase 2 NCT03972592 France
Water
Fujino Akihiro
2016 - JPRN-jRCTs031180265 -