294. 先天性横隔膜ヘルニア Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 18 / 薬物数 : 31 - (DrugBank : 5) / 標的遺伝子数 : 5 - 標的パスウェイ数 : 13
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Autologous umbilical cord blood
The University of Texas Health Science Center, Houston
2018 Phase 1 NCT03526588 United States
Blood sample
Assistance Publique - Hôpitaux de Paris
2014 - NCT02175264 France
Bronchodilator response
The Hospital for Sick Children
2012 - NCT02453750 Canada
DE-implementation OF inhaled nitric oxide (INO) USE
The University of Texas Health Science Center, Houston
2025 Phase 4 NCT05213676 United States
Fecal microbiome probiotic
Medical University of Graz
2018 - NCT03787160 Austria
Functional residual capacity
Medical University of Graz
2018 - NCT03787160 Austria
Hypersaline
The Hospital for Sick Children
2012 - NCT02453750 Canada
Inalossin - 800 PPM MOL/MOL GAS medicinale compresso bombola IN alluminio CON valvola VI DA 20 litri
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Inalossin 800 PPM MOL/MOL GAS medicinale compresso
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Initial fecal microbiome
Medical University of Graz
2018 - NCT03787160 Austria
Initial pulmonary microbiome
Medical University of Graz
2018 - NCT03787160 Austria
Initial VOC
Medical University of Graz
2018 - NCT03787160 Austria
Inomax 800PPM MOL/MOL inhalatiegas
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
2017 Phase 3 EUCTR2017-000421-13-NL Austria;Belgium;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Lipid injectable emulsion with fish OIL
Coordinación de Investigación en Salud, Mexico
2019 Phase 2 NCT04031508 Mexico
Losec
ErasmusMC
2013 - EUCTR2013-002026-22-NL Netherlands
Maximum oxygen uptake
Medical University of Graz
2018 - NCT03787160 Austria
Milrinone
NICHD Neonatal Research Network
2017 Phase 2 NCT02951130 United States
Neophyr 1000PPM MOL/MOL
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
Nitric oxide
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Omeprazol
ErasmusMC
2013 - EUCTR2013-002026-22-NL Netherlands
Omeprazole rectally 1MG/KG
Rijnstate Hospital
2005 Phase 3 NCT00226044 Netherlands
Ossido DI azoto
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Probiotic treatment
Medical University of Graz
2018 - NCT03787160 Austria
Pulmonary microbiome probiotic
Medical University of Graz
2018 - NCT03787160 Austria
Repair OF CDH W/alloderm
Children's Mercy Hospital Kansas City
2005 Phase 3 NCT00257946 United States
Repair OF CDH W/SIS gold
Children's Mercy Hospital Kansas City
2005 Phase 3 NCT00257946 United States
Revatio - 0.8 MG/ML - soluzione iniettabile - USO endovenoso - flaconcino(vetro) 1 flaconcino DA 20 ML
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Revatio 0.8MG/ML solution FOR injection
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
2017 Phase 3 EUCTR2017-000421-13-NL Austria;Belgium;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Sildenafil
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Erasmus MC
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
Xinhua Hospital Affiliated to Shanghai Jiaotong University School of Medicine
2020 Phase 0 ChiCTR2000037331 China
Sildenafil oral suspension
University of Utah
2022 Phase 2 NCT05201144 United States
VOC probiotic
Medical University of Graz
2018 - NCT03787160 Austria
The University of Texas Health Science Center, Houston
2018 Phase 1 NCT03526588 United States
Blood sample
Assistance Publique - Hôpitaux de Paris
2014 - NCT02175264 France
Bronchodilator response
The Hospital for Sick Children
2012 - NCT02453750 Canada
DE-implementation OF inhaled nitric oxide (INO) USE
The University of Texas Health Science Center, Houston
2025 Phase 4 NCT05213676 United States
Fecal microbiome probiotic
Medical University of Graz
2018 - NCT03787160 Austria
Functional residual capacity
Medical University of Graz
2018 - NCT03787160 Austria
Hypersaline
The Hospital for Sick Children
2012 - NCT02453750 Canada
Inalossin - 800 PPM MOL/MOL GAS medicinale compresso bombola IN alluminio CON valvola VI DA 20 litri
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Inalossin 800 PPM MOL/MOL GAS medicinale compresso
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Initial fecal microbiome
Medical University of Graz
2018 - NCT03787160 Austria
Initial pulmonary microbiome
Medical University of Graz
2018 - NCT03787160 Austria
Initial VOC
Medical University of Graz
2018 - NCT03787160 Austria
Inomax 800PPM MOL/MOL inhalatiegas
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
2017 Phase 3 EUCTR2017-000421-13-NL Austria;Belgium;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Lipid injectable emulsion with fish OIL
Coordinación de Investigación en Salud, Mexico
2019 Phase 2 NCT04031508 Mexico
Losec
ErasmusMC
2013 - EUCTR2013-002026-22-NL Netherlands
Maximum oxygen uptake
Medical University of Graz
2018 - NCT03787160 Austria
Milrinone
NICHD Neonatal Research Network
2017 Phase 2 NCT02951130 United States
Neophyr 1000PPM MOL/MOL
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
Nitric oxide
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Omeprazol
ErasmusMC
2013 - EUCTR2013-002026-22-NL Netherlands
Omeprazole rectally 1MG/KG
Rijnstate Hospital
2005 Phase 3 NCT00226044 Netherlands
Ossido DI azoto
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Probiotic treatment
Medical University of Graz
2018 - NCT03787160 Austria
Pulmonary microbiome probiotic
Medical University of Graz
2018 - NCT03787160 Austria
Repair OF CDH W/alloderm
Children's Mercy Hospital Kansas City
2005 Phase 3 NCT00257946 United States
Repair OF CDH W/SIS gold
Children's Mercy Hospital Kansas City
2005 Phase 3 NCT00257946 United States
Revatio - 0.8 MG/ML - soluzione iniettabile - USO endovenoso - flaconcino(vetro) 1 flaconcino DA 20 ML
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Revatio 0.8MG/ML solution FOR injection
Erasmus MC
2019 Phase 3 EUCTR2017-000421-13-BE Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 3 EUCTR2017-000421-13-NO Austria;Belgium;Italy;Netherlands;Norway;Sweden
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
2017 Phase 3 EUCTR2017-000421-13-NL Austria;Belgium;Netherlands;Norway;Sweden
- Phase 3 EUCTR2017-000421-13-SE Austria;Belgium;Netherlands;Norway;Sweden
Sildenafil
ERASMUS MEDICAL CENTER
2020 Phase 3 EUCTR2017-000421-13-IT Austria;Belgium;Germany;Italy;Netherlands;Norway;Spain;Sweden
Erasmus MC
2018 Phase 4 EUCTR2017-000421-13-AT Austria;Belgium;Italy;Netherlands;Norway;Sweden
Xinhua Hospital Affiliated to Shanghai Jiaotong University School of Medicine
2020 Phase 0 ChiCTR2000037331 China
Sildenafil oral suspension
University of Utah
2022 Phase 2 NCT05201144 United States
VOC probiotic
Medical University of Graz
2018 - NCT03787160 Austria