316. カルニチン回路異常症 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 4 / 薬物数 : 12 - (DrugBank : 2) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 11

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Bezafibrate
   Assistance Publique - Hôpitaux de Paris
      2006   Phase 3   NCT00336167   France
   Rigshospitalet, Denmark
      2009   Phase 2   NCT00983788   Denmark
Glycerol/saline
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Hyperinsulinemic euglycemic clamp
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Intralipid/heparin
   Oregon Health and Science University
      2016   -   NCT02517307   United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan