325. 遺伝性自己炎症疾患 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 12 / 薬物数 : 15 - (DrugBank : 7) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 37
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
3TC
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
Abacavir
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
ABC
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
AZT
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
Baricitinib
Adeline Vanderver, MD
2019 Phase 2 NCT03921554 United States
Eli Lilly and Company
2020 Phase 2/Phase 3 NCT04517253 Japan
2012 - NCT01724580 United Kingdom;United States
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
- Phase 2 EUCTR2015-003424-31-GB France;United Kingdom;United States
Censavudine
Transposon Therapeutics Inc
2022 Phase 2 EUCTR2022-000064-21-IT France;Italy;United Kingdom
Transposon Therapeutics, Inc
2023 Phase 2 EUCTR2022-000064-21-FR France;Italy;United Kingdom
Emtricitabine
Children's Hospital of Philadelphia
2025 Phase 1/Phase 2 NCT03304717 United States
JAK inhibitor
IRCCS Fondazione Stella Maris
2024 - NCT06898372 Italy
Lamivudine
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
LY3009104
Eli Lilly and Company
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
- Phase 2 EUCTR2015-003424-31-GB France;United Kingdom;United States
Olumiant
Eli Lilly and Company
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
Reverse transcriptase inhibitors: zidovudine, lamivudine, abacavir
Assistance Publique - Hôpitaux de Paris
2015 Phase 2 NCT02363452 France
Tenofovir
Children's Hospital of Philadelphia
2025 Phase 1/Phase 2 NCT03304717 United States
TPN-101
Transposon Therapeutics Inc
2022 Phase 2 EUCTR2022-000064-21-IT France;Italy;United Kingdom
Transposon Therapeutics, Inc
2023 Phase 2 EUCTR2022-000064-21-FR France;Italy;United Kingdom
Transposon Therapeutics, Inc.
2023 Phase 2 NCT05613868 France;Italy;United Kingdom
Zidovudine
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
Abacavir
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
ABC
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
AZT
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
Baricitinib
Adeline Vanderver, MD
2019 Phase 2 NCT03921554 United States
Eli Lilly and Company
2020 Phase 2/Phase 3 NCT04517253 Japan
2012 - NCT01724580 United Kingdom;United States
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
- Phase 2 EUCTR2015-003424-31-GB France;United Kingdom;United States
Censavudine
Transposon Therapeutics Inc
2022 Phase 2 EUCTR2022-000064-21-IT France;Italy;United Kingdom
Transposon Therapeutics, Inc
2023 Phase 2 EUCTR2022-000064-21-FR France;Italy;United Kingdom
Emtricitabine
Children's Hospital of Philadelphia
2025 Phase 1/Phase 2 NCT03304717 United States
JAK inhibitor
IRCCS Fondazione Stella Maris
2024 - NCT06898372 Italy
Lamivudine
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom
LY3009104
Eli Lilly and Company
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
- Phase 2 EUCTR2015-003424-31-GB France;United Kingdom;United States
Olumiant
Eli Lilly and Company
- Phase 2;Phase 3 EUCTR2025-000001-16-Outside-EU/EEA Japan
Reverse transcriptase inhibitors: zidovudine, lamivudine, abacavir
Assistance Publique - Hôpitaux de Paris
2015 Phase 2 NCT02363452 France
Tenofovir
Children's Hospital of Philadelphia
2025 Phase 1/Phase 2 NCT03304717 United States
TPN-101
Transposon Therapeutics Inc
2022 Phase 2 EUCTR2022-000064-21-IT France;Italy;United Kingdom
Transposon Therapeutics, Inc
2023 Phase 2 EUCTR2022-000064-21-FR France;Italy;United Kingdom
Transposon Therapeutics, Inc.
2023 Phase 2 NCT05613868 France;Italy;United Kingdom
Zidovudine
University of Edinburgh
2022 Phase 2 NCT04731103 United Kingdom