325. 遺伝性自己炎症疾患 Disease details / Clinical trials / Drug dev / DR info


臨床試験数 : 12 / 薬物数 : 15 - (DrugBank : 7) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 37

薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
3TC
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom
Abacavir
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom
ABC
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom
AZT
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom
Baricitinib
   Adeline Vanderver, MD
      2019   Phase 2   NCT03921554   United States
   Eli Lilly and Company
      2020   Phase 2/Phase 3   NCT04517253   Japan
      2012   -   NCT01724580   United Kingdom;United States
      -   Phase 2;Phase 3   EUCTR2025-000001-16-Outside-EU/EEA   Japan
      -   Phase 2   EUCTR2015-003424-31-GB   France;United Kingdom;United States
Censavudine
   Transposon Therapeutics Inc
      2022   Phase 2   EUCTR2022-000064-21-IT   France;Italy;United Kingdom
   Transposon Therapeutics, Inc
      2023   Phase 2   EUCTR2022-000064-21-FR   France;Italy;United Kingdom
Emtricitabine
   Children's Hospital of Philadelphia
      2025   Phase 1/Phase 2   NCT03304717   United States
JAK inhibitor
   IRCCS Fondazione Stella Maris
      2024   -   NCT06898372   Italy
Lamivudine
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom
LY3009104
   Eli Lilly and Company
      -   Phase 2;Phase 3   EUCTR2025-000001-16-Outside-EU/EEA   Japan
      -   Phase 2   EUCTR2015-003424-31-GB   France;United Kingdom;United States
Olumiant
   Eli Lilly and Company
      -   Phase 2;Phase 3   EUCTR2025-000001-16-Outside-EU/EEA   Japan
Reverse transcriptase inhibitors: zidovudine, lamivudine, abacavir
   Assistance Publique - Hôpitaux de Paris
      2015   Phase 2   NCT02363452   France
Tenofovir
   Children's Hospital of Philadelphia
      2025   Phase 1/Phase 2   NCT03304717   United States
TPN-101
   Transposon Therapeutics Inc
      2022   Phase 2   EUCTR2022-000064-21-IT   France;Italy;United Kingdom
   Transposon Therapeutics, Inc
      2023   Phase 2   EUCTR2022-000064-21-FR   France;Italy;United Kingdom
   Transposon Therapeutics, Inc.
      2023   Phase 2   NCT05613868   France;Italy;United Kingdom
Zidovudine
   University of Edinburgh
      2022   Phase 2   NCT04731103   United Kingdom