12. Congenital myasthenic syndrome Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 7 /  Drugs : 8 - (DrugBank : 3) / Drug target genes : 8 - Drug target pathways : 16

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
3,4-diaminopyridine
   Lahey Clinic
      2001   -   NCT00872950   United States
   Ricardo Maselli
      2017   -   NCT03062631   United States
   Vern C. Juel, M.D.
      2012   -   NCT01765140   United States
Albuterol
   Mayo Clinic
      2010   Phase 1   NCT01203592   United States
Alloex exosomes
   The Foundation for Orthopaedics and Regenerative Medicine
      2025   Phase 1   NCT07226726   Antigua and Barbuda;United States
Amifampridine phosphate
   Catalyst Pharmaceuticals, Inc.
      2015   -   NCT02189720   United States
ARGX-119
   argenx
      2024   Phase 1   NCT06436742   Canada;France;Italy;Spain;United Kingdom;United States