131. Alexander disease Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 4 / Drugs : 4 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0
Other names | ALXDRD;AxD; | ||
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Disease group | Neuromuscular diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
52 patients Age distribution
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 11-8-25. Alexander disease | ||
Subtypes | No. | Name | Specific pediatric chronic diseases, Japan (in Japanese) |
131-1. | Alexander Disease type 1;ALXDRD1;AxD1; | 11-8-25. Alexander disease | |
131-2. | Alexander Disease type 2;ALXDRD2;AxD2; | 11-8-25. Alexander disease | |
131-3. | Alexander disease type 3;ALXDRD3;AxD3; | 11-8-25. Alexander disease |