139. Congenital cerebral hypomyelination Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 13 / Drugs : 8 - (DrugBank : 4) / Drug target genes : 2 - Drug target pathways : 3
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Curcumin
Inoue Ken
2018 - JPRN-jRCTs031180348 -
Deferiprone
VU University Medical Center
2022 Phase 2 EUCTR2021-000070-29-NL Netherlands
Hucns-SC cells
StemCells, Inc.
2009 Phase 1 NCT01005004 United States
Hucns-SC transplant IN THE LEAD-IN phase
StemCells, Inc.
2011 - NCT01391637 United States
ION356
Ionis Pharmaceuticals, Inc.
2024 Phase 1 NCT06150716 France;Germany;Japan;Netherlands;United States
Tiratricol
Erasmus Medical Centre
2016 Phase 2 EUCTR2014-000178-20-IT Belgium;Czech Republic;France;Germany;Italy
2016 Phase 2 EUCTR2014-000178-20-FR Australia;Belgium;Canada;Czech Republic;France;Germany;Italy;South Africa
2016 Phase 2 EUCTR2014-000178-20-CZ Belgium;Czech Republic;Germany;Italy
2015 Phase 2 EUCTR2014-000178-20-BE Australia;Belgium;Canada;Chile;Czech Republic;France;Germany;Italy;South Africa
- Phase 2 EUCTR2014-000178-20-DE Australia;Belgium;Canada;Czech Republic;France;Germany;Israel;Italy;South Africa
Rare Thyroid Therapeutics International AB
2023 - NCT05911399 United States
2023 Phase 3 NCT05579327 Netherlands;United Kingdom;United States
Triac
Rare Thyroid Therapeutics International AB
2020 Phase 2 NCT02396459 Czechia;Germany;Netherlands;United States
Téatrois
Erasmus Medical Centre
2016 Phase 2 EUCTR2014-000178-20-IT Belgium;Czech Republic;France;Germany;Italy
2016 Phase 2 EUCTR2014-000178-20-FR Australia;Belgium;Canada;Czech Republic;France;Germany;Italy;South Africa
2016 Phase 2 EUCTR2014-000178-20-CZ Belgium;Czech Republic;Germany;Italy
2015 Phase 2 EUCTR2014-000178-20-BE Australia;Belgium;Canada;Chile;Czech Republic;France;Germany;Italy;South Africa
- Phase 2 EUCTR2014-000178-20-DE Australia;Belgium;Canada;Czech Republic;France;Germany;Israel;Italy;South Africa
Inoue Ken
2018 - JPRN-jRCTs031180348 -
Deferiprone
VU University Medical Center
2022 Phase 2 EUCTR2021-000070-29-NL Netherlands
Hucns-SC cells
StemCells, Inc.
2009 Phase 1 NCT01005004 United States
Hucns-SC transplant IN THE LEAD-IN phase
StemCells, Inc.
2011 - NCT01391637 United States
ION356
Ionis Pharmaceuticals, Inc.
2024 Phase 1 NCT06150716 France;Germany;Japan;Netherlands;United States
Tiratricol
Erasmus Medical Centre
2016 Phase 2 EUCTR2014-000178-20-IT Belgium;Czech Republic;France;Germany;Italy
2016 Phase 2 EUCTR2014-000178-20-FR Australia;Belgium;Canada;Czech Republic;France;Germany;Italy;South Africa
2016 Phase 2 EUCTR2014-000178-20-CZ Belgium;Czech Republic;Germany;Italy
2015 Phase 2 EUCTR2014-000178-20-BE Australia;Belgium;Canada;Chile;Czech Republic;France;Germany;Italy;South Africa
- Phase 2 EUCTR2014-000178-20-DE Australia;Belgium;Canada;Czech Republic;France;Germany;Israel;Italy;South Africa
Rare Thyroid Therapeutics International AB
2023 - NCT05911399 United States
2023 Phase 3 NCT05579327 Netherlands;United Kingdom;United States
Triac
Rare Thyroid Therapeutics International AB
2020 Phase 2 NCT02396459 Czechia;Germany;Netherlands;United States
Téatrois
Erasmus Medical Centre
2016 Phase 2 EUCTR2014-000178-20-IT Belgium;Czech Republic;France;Germany;Italy
2016 Phase 2 EUCTR2014-000178-20-FR Australia;Belgium;Canada;Czech Republic;France;Germany;Italy;South Africa
2016 Phase 2 EUCTR2014-000178-20-CZ Belgium;Czech Republic;Germany;Italy
2015 Phase 2 EUCTR2014-000178-20-BE Australia;Belgium;Canada;Chile;Czech Republic;France;Germany;Italy;South Africa
- Phase 2 EUCTR2014-000178-20-DE Australia;Belgium;Canada;Czech Republic;France;Germany;Israel;Italy;South Africa